Gene therapies for inherited retinal disorders

Visual Neuroscience

Volumn 31, Issue , 2014, Pages 289-307

  Farrar, G Jane ^a   Millington Ward, Sophia ^a   Chadderton, Naomi ^a   Mansergh, Fiona C ^a   Palfi, Arpad ^a  

^a TRINITY COLLEGE DUBLIN   (Ireland)

Author keywords

Adeno associated virus; Gene therapy; Optogenetics; Retinal degenerations; RNA interference

Indexed keywords

LENTIVIRUS VECTOR; NEUROTROPHIC FACTOR; RHODOPSIN;

ADENO ASSOCIATED VIRUS; ALZHEIMER DISEASE; APOPTOSIS; AUTOSOMAL DOMINANT INHERITANCE; AUTOSOMAL DOMINANT OPTIC ATROPHY; AUTOSOMAL RECESSIVE DISORDER; BARDET BIEDL SYNDROME; BRAIN DEGENERATION; CELL STRESS; CELL THERAPY; CHOROIDEREMIA; DIABETIC RETINOPATHY; DISEASE COURSE; DISORDERS OF MITOCHONDRIAL FUNCTIONS; DOMINANT INHERITANCE; GENE REPLACEMENT THERAPY; GENE REPRESSION; GENE TARGETING; GENE THERAPY; GENETIC DISORDER; HAPLOINSUFFICIENCY; HOMOLOGOUS RECOMBINATION; HUMAN; HUNTINGTON CHOREA; LEBER HEREDITARY OPTIC NEUROPATHY; MOLECULAR PATHOLOGY; NONHUMAN; OPTOGENETICS; OXIDATIVE STRESS; PHASE 1 CLINICAL TRIAL (TOPIC); PHASE 2 CLINICAL TRIAL (TOPIC); PHASE 3 CLINICAL TRIAL (TOPIC); PROMOTER REGION; RETINA CELL; RETINA DISEASE; RETINA DYSTROPHY; RETINOPATHY; REVIEW; RNA INTERFERENCE; STARGARDT DISEASE; USHER SYNDROME; VIRAL GENE THERAPY; VITELLIFORM MACULAR DEGENERATION; ANIMAL; GENETICS; RETINAL DISEASES;

ANIMALS; GENETIC THERAPY; HUMANS; RETINAL DISEASES;

EID: 84911383810     PISSN: 09525238     EISSN: 14698714     Source Type: Journal    
DOI: 10.1017/S0952523814000133     Document Type: Review

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