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Volumn 935, Issue , 2013, Pages 351-369

Adeno-associated viral vectors for gene therapy of inherited retinal degenerations

Author keywords

Adeno associated virus; Gene transfer; Retinal degeneration

Indexed keywords

ADENO ASSOCIATED VIRUS; ANIMAL; ARTICLE; GENE THERAPY; GENE TRANSFER; GENE VECTOR; GENETICS; HUMAN; METHODOLOGY; RETINA DEGENERATION;

EID: 84871945466     PISSN: 10643745     EISSN: None     Source Type: Book Series    
DOI: 10.1007/978-1-62703-080-9-25     Document Type: Article
Times cited : (22)

References (31)
  • 1
    • 78650902662 scopus 로고    scopus 로고
    • Optogenetics
    • Deisseroth K (2011) Optogenetics. Nat Methods 8(1):26-29
    • (2011) Nat Methods , vol.8 , Issue.1 , pp. 26-29
    • Deisseroth, K.1
  • 5
    • 79955116220 scopus 로고    scopus 로고
    • Genetic visualization with an improved GCaMP calcium indicator reveals spatiotemporal activation of the spinal motor neurons in zebra fish
    • Muto A, Ohkura M, Kotani T, Higashijima S, Nakai J, Kawakami K (2011) Genetic visualization with an improved GCaMP calcium indicator reveals spatiotemporal activation of the spinal motor neurons in zebra fi sh Proc Natl Acad Sci U S A 108(13):5425-5430
    • (2011) Proc Natl Acad Sci U S A , vol.108 , Issue.13 , pp. 5425-5430
    • Muto, A.1    Ohkura, M.2    Kotani, T.3    Higashijima, S.4    Nakai, J.5    Kawakami, K.6
  • 6
    • 79951713532 scopus 로고    scopus 로고
    • Differential targeting of optical neuromodulators to ganglion cell soma and dendrites allows dynamic control of center-surround antagonism
    • Greenberg KP, Pham A, Werblin FS (2011) Differential targeting of optical neuromodulators to ganglion cell soma and dendrites allows dynamic control of center-surround antagonism. Neuron 69(4):713-720
    • (2011) Neuron , vol.69 , Issue.4 , pp. 713-720
    • Greenberg, K.P.1    Pham, A.2    Werblin, F.S.3
  • 7
    • 2642642141 scopus 로고    scopus 로고
    • Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus
    • Xiao X, Li J, Samulski RJ (1998) Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus. J Virol 72(3):2224-2232 (Pubitemid 28100780)
    • (1998) Journal of Virology , vol.72 , Issue.3 , pp. 2224-2232
    • Xiao, X.1    Juan, L.I.2    Samulski, R.J.3
  • 9
    • 74049085498 scopus 로고    scopus 로고
    • Effect of genome size on AAV vector packaging
    • Wu Z, Yang H, Colosi P (2010) Effect of genome size on AAV vector packaging. Mol Ther 18(1):80-86
    • (2010) Mol Ther , vol.18 , Issue.1 , pp. 80-86
    • Wu, Z.1    Yang, H.2    Colosi, P.3
  • 10
    • 74049092844 scopus 로고    scopus 로고
    • Characterization of genome integrity for oversized recombinant AAV vector
    • Dong B, Nakai H, Xiao W (2010) Characterization of genome integrity for oversized recombinant AAV vector. Mol Ther 18(1):87-92
    • (2010) Mol Ther , vol.18 , Issue.1 , pp. 87-92
    • Dong, B.1    Nakai, H.2    Xiao, W.3
  • 13
    • 35848961457 scopus 로고    scopus 로고
    • Systemic AAV-9 transduction in mice is influenced by animal age but not by the route of administration
    • DOI 10.1038/sj.gt.3303029, PII 3303029
    • Bostick B, Ghosh A, Yue Y, Long C, Duan D (2007) Systemic AAV-9 transduction in mice is in fl uenced by animal age but not by the route of administration. Gene Ther 14(22): 1605-1609 (Pubitemid 350056232)
    • (2007) Gene Therapy , vol.14 , Issue.22 , pp. 1605-1609
    • Bostick, B.1    Ghosh, A.2    Yue, Y.3    Long, C.4    Duan, D.5
  • 14
    • 0032870158 scopus 로고    scopus 로고
    • Genetic capsid modifications allow efficient re-targeting of adeno- associated virus type 2
    • DOI 10.1038/12491
    • Girod A, Ried M, Wobus C, Lahm H, Leike K, Kleinschmidt J, Deleage G, Hallek M (1999) Genetic capsid modi fi cations allow ef fi cient retargeting of adeno-associated virus type 2. Nat Med 5(9):1052-1056 (Pubitemid 29439578)
    • (1999) Nature Medicine , vol.5 , Issue.9 , pp. 1052-1056
    • Girod, A.1    Ried, M.2    Wobus, C.3    Lahm, H.4    Leike, K.5    Kleinschmidt, J.6    Deleage, G.7    Hallek, M.8
  • 17
    • 70449338146 scopus 로고    scopus 로고
    • A novel adeno-associated viral variant for ef fi cient and selective intravitreal transduction of rat Muller cells
    • Klimczak RR, Koerber JT, Dalkara D, Flannery JG, Schaffer DV (2009) A novel adeno-associated viral variant for ef fi cient and selective intravitreal transduction of rat Muller cells. PLoS One 4(10):e7467
    • (2009) PLoS One , vol.4 , Issue.10
    • Klimczak, R.R.1    Koerber, J.T.2    Dalkara, D.3    Flannery, J.G.4    Schaffer, D.V.5
  • 20
    • 0036805547 scopus 로고    scopus 로고
    • Fast and reliable titration of recombinant adeno-associated virus type-2 using quantitative real-time PCR
    • DOI 10.1016/S0166-0934(02)00138-6, PII S0166093402001386
    • Rohr UP, Wulf MA, Stahn S, Steidl U, Haas R, Kronenwett R (2002) Fast and reliable titration of recombinant adeno-associated virus type-2 using quantitative real-time PCR. J Virol Methods 106(1):81-88 (Pubitemid 35279652)
    • (2002) Journal of Virological Methods , vol.106 , Issue.1 , pp. 81-88
    • Rohr, U.-P.1    Wulf, M.-A.2    Stahn, S.3    Steidl, U.4    Haas, R.5    Kronenwett, R.6
  • 22
    • 0023665902 scopus 로고
    • An analysis of 5 ¢ noncoding sequences from 699 vertebrate messenger RNAs
    • Kozak M (1987) An analysis of 5 ¢ -noncoding sequences from 699 vertebrate messenger RNAs. Nucleic Acid Res 15(20):8125-8148
    • (1987) Nucleic Acid Res , vol.15 , Issue.20 , pp. 8125-8148
    • Kozak, M.1
  • 23
    • 0033588890 scopus 로고    scopus 로고
    • Enhanced expression of transgenes from adeno-associated virus vectors with the woodchuck hepatitis virus posttranscriptional regulatory element: Implications for gene therapy
    • DOI 10.1089/10430349950016942
    • Loeb JE, Cordier WS, Harris ME, Weitzman MD, Hope TJ (1999) Enhanced expression of transgenes from adeno-associated virus vectors with the woodchuck hepatitis virus posttranscriptional regulatory element: Implications for gene therapy. Hum Gene Ther 10(14): 2295-2305 (Pubitemid 29459840)
    • (1999) Human Gene Therapy , vol.10 , Issue.14 , pp. 2295-2305
    • Loeb, J.E.1    Cordier, W.S.2    Harris, M.E.3    Weitzman, M.D.4    Hope, T.J.5
  • 25
    • 34347252689 scopus 로고    scopus 로고
    • Production and characterization of adenoassociated viral vectors
    • Grieger JC, Choi VW, Samulski RJ (2006) Production and characterization of adenoassociated viral vectors. Nat Protoc 1(3): 1412-1428
    • (2006) Nat Protoc , vol.1 , Issue.3 , pp. 1412-1428
    • Grieger, J.C.1    Choi, V.W.2    Samulski, R.J.3
  • 27
    • 77958083331 scopus 로고    scopus 로고
    • Ef fi cient serotypedependent release of functional vector into the culture medium during adeno-associated virus manufacturing
    • Vandenberghe LH, Xiao R, Lock M, Lin J, Korn M, Wilson JM (2010) Ef fi cient serotypedependent release of functional vector into the culture medium during adeno-associated virus manufacturing. Hum Gene Ther 21(10): 1251-1257
    • (2010) Hum Gene Ther , vol.21 , Issue.10 , pp. 1251-1257
    • Vandenberghe, L.H.1    Xiao, R.2    Lock, M.3    Lin, J.4    Korn, M.5    Wilson, J.M.6


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.