AAV delivery of wild-type rhodopsin preserves retinal function in a mouse model of autosomal dominant retinitis pigmentosa

Human Gene Therapy

Volumn 22, Issue 5, 2011, Pages 567-575

  Mao, Haoyu ^a   James, Thomas ^a   Schwein, Alison ^a   Shabashvili, Arseniy E ^a   Hauswirth, William W ^a,b   Gorbatyuk, Marina S ^a,c   Lewin, Alfred S ^a  

^a UNIVERSITY OF FLORIDA   (United States)

^b UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

^c UNIVERSITY OF NORTH TEXAS HEALTH SCIENCE CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; COMPLEMENTARY DNA; OPSIN; RHODOPSIN;

ADENOVIRUS 5; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; AUTOSOMAL DOMINANT RETINITIS PIGMENTOSA; CONTROLLED STUDY; ELECTRORETINOGRAPHY; GENE EXPRESSION; GENE MUTATION; GENETIC ANALYSIS; MOLECULAR CLONING; MOUSE; NONHUMAN; NUCLEOTIDE SEQUENCE; PHOTORECEPTOR; PROMOTER REGION; RAT; RETINA DEGENERATION; RETINITIS PIGMENTOSA; THICKNESS; TRANSGENE;

ANIMALS; CLONING, MOLECULAR; DEPENDOVIRUS; DNA PRIMERS; DNA, COMPLEMENTARY; ELECTRORETINOGRAPHY; GENE THERAPY; GENES, DOMINANT; GENETIC VECTORS; IMMUNOBLOTTING; MICE; MICE, TRANSGENIC; RETINA; RETINITIS PIGMENTOSA; REVERSE TRANSCRIPTASE POLYMERASE CHAIN REACTION; RHODOPSIN;

ADENO-ASSOCIATED VIRUS; MUS; MUS MUSCULUS;

EID: 79955372235     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2010.140     Document Type: Article

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