AAV-mediated cone rescue in a naturally occurring mouse model of CNGA3-achromatopsia

PLoS ONE

Volumn 7, Issue 4, 2012, Pages

  Pang, Ji jing ^a,b   Deng, Wen Tao ^a   Dai, Xufeng ^a,b   Lei, Bo ^c   Everhart, Drew ^d   Umino, Yumiko ^d   Li, Jie ^a   Zhang, Keqing ^c   Mao, Song ^a   Boye, Sanford L ^a   Liu, Li ^a   Chiodo, Vince A ^a   Liu, Xuan ^a   Shi, Wei ^a   Tao, Ye ^a   Chang, Bo ^e   Hauswirth, William W ^a  

^a UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

^b WENZHOU MEDICAL UNIVERSITY   (China)

^c THE FIRST AFFILIATED HOSPITAL OF CHONGQING MEDICAL UNIVERSITY   (China)

^d SUNY UPSTATE MEDICAL UNIVERSITY   (United States)

^e JACKSON LABORATORY   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

CONE OPSIN; CYCLIC NUCLEOTIDE GATED CHANNEL; PARVOVIRUS VECTOR; CNGA3 PROTEIN, MOUSE; OPSIN;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; COLOR BLINDNESS; CONTRAST SENSITIVITY; CONTROLLED STUDY; DRUG ADMINISTRATION ROUTE; GENE MUTATION; GENE REPLACEMENT THERAPY; LIGHT; MOUSE; MOUSE STRAIN; NONHUMAN; PATHOGENESIS; PROTEIN EXPRESSION; PROTEIN LOCALIZATION; RETINA CONE; RETINA DEGENERATION; SUBRETINAL INJECTION; THERAPY EFFECT; VISUAL ACUITY; VISUAL IMPAIRMENT; ADENO ASSOCIATED VIRUS; ANIMAL; COLOR VISION DEFECT; DISEASE MODEL; ELECTRORETINOGRAPHY; GENE EXPRESSION REGULATION; GENE THERAPY; GENE VECTOR; GENETICS; HUMAN; METABOLISM; MUTATION; PATHOLOGY;

ANIMALS; COLOR VISION DEFECTS; CYCLIC NUCLEOTIDE-GATED CATION CHANNELS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; ELECTRORETINOGRAPHY; GENE EXPRESSION REGULATION; GENE THERAPY; GENETIC VECTORS; HUMANS; MICE; MUTATION; OPSINS; RETINAL CONE PHOTORECEPTOR CELLS;

EID: 84859612115     PISSN: None     EISSN: 19326203     Source Type: Journal    
DOI: 10.1371/journal.pone.0035250     Document Type: Article

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