Erratum: Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors (Human Molecular Genetics (2009) 18: 12 (2099–2114) DOI: 10.1093/hmg/ddp133);Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1: Effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors

Human Molecular Genetics

Volumn 18, Issue 12, 2009, Pages 2099-2114

  Tan, Mei Hong ^a   Smith, Alexander J ^a   Pawlyk, Basil ^b   Xu, Xiaoyun ^b   Liu, Xiaoqing ^b   Bainbridge, James B ^a   Basche, Mark ^a   McIntosh, Jenny ^c   Tran, Hoai Viet ^a   Nathwani, Amit ^c   Li, Tiansen ^b   Ali, Robin R ^a,b,d  

^a UNIVERSITY COLLEGE LONDON   (United Kingdom)

^b HARVARD MEDICAL SCHOOL   (United States)

^c INSTITUTE OF CANCER RESEARCH   (United Kingdom)

^d NONE   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; AROMATIC HYDROCARBON RECEPTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CELL FUNCTION; CELL SURVIVAL; CONTROLLED STUDY; DISEASE COURSE; GENE REPLACEMENT THERAPY; GENE TARGETING; GENE THERAPY; GENE TRANSFER; GENETIC TRANSDUCTION; HUMAN; LEBER CONGENITAL AMAUROSIS; MOUSE; NONHUMAN; PHOTORECEPTOR; PRIORITY JOURNAL; PROTEIN FUNCTION; RETINA DEGENERATION; RETINITIS PIGMENTOSA; TREATMENT RESPONSE; VIRAL GENE DELIVERY SYSTEM;

ADENO-ASSOCIATED VIRUS; MUS;

EID: 66149101630     PISSN: 09646906     EISSN: 14602083     Source Type: Journal    
DOI: 10.1093/hmg/ddad169     Document Type: Erratum

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