Ribozyme rescue of photoreceptor cells in P23H transgenic rats: Long-term survival and late-stage therapy

Proceedings of the National Academy of Sciences of the United States of America

Volumn 97, Issue 21, 2000, Pages 11488-11493

  LaVail, Matthew M ^a,d   Yasumura, Douglas ^a   Matthes, Michael T ^a   Drenser, Kimberly A ^a,c   Flannery, John G ^b   Lewin, Alfred S ^c   Hauswirth, William W ^c  

^a UNIVERSITY OF CALIFORNIA   (United States)

^b UNIVERSITY OF CALIFORNIA   (United States)

^c UNIVERSITY OF FLORIDA   (United States)

^d UNIVERSITY OF CALIFORNIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

VIRUS VECTOR;

ADENOVIRUS; ANIMAL CELL; ANIMAL MODEL; AUTOSOMAL DOMINANT DISORDER; CONFERENCE PAPER; CONTROLLED STUDY; ELECTRORETINOGRAPHY; GENE THERAPY; GENE TRANSFER; NONHUMAN; PHOTORECEPTOR CELL; PRIORITY JOURNAL; PROMOTER REGION; RAT; RETINA DEGENERATION; RETINA DISEASE; SURVIVAL RATE; TRANSGENIC MOUSE;

ADENO-ASSOCIATED VIRUS; ADENOVIRIDAE; ANIMALIA; BOVINAE; MUS MUSCULUS;

EID: 0034633619     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.210319397     Document Type: Article

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