Strategems in vitro for gene therapies directed to dominant mutations

Human Molecular Genetics

Volumn 6, Issue 9, 1997, Pages 1415-1426

  Millington Ward, Sophia ^a   O'Neill, Brian ^a   Tuohy, Gearoid ^a   Al Jandal, Najma ^a   Kiang, Anna Sophia ^a   Kenna, Paul F ^a   Palfi, Arpad ^b   Hayden, Patrick ^a   Mansergh, Fiona ^a   Kennan, Avril ^a   Humphries, Peter ^a   Farrar, G Jane ^a  

^a TRINITY COLLEGE DUBLIN   (Ireland)

^b UNIVERSITY OF SZEGED   (Hungary)

Author keywords

[No Author keywords available]

Indexed keywords

COLLAGEN; MESSENGER RNA; MUTANT PROTEIN; PERIPHERIN; RHODOPSIN; RIBOZYME;

ALLELE; ARTICLE; AUTOSOMAL DOMINANT DISORDER; DNA POLYMORPHISM; GENE; GENE REPRESSION; GENE THERAPY; GENETIC CODE; GENETIC HETEROGENEITY; GENETIC TRANSCRIPTION; HUMAN; MOUSE; NONHUMAN; PRIORITY JOURNAL; RNA CLEAVAGE; TECHNIQUE;

ALLELES; ANIMALS; APOPTOSIS; COLLAGEN; GENE EXPRESSION; GENE TARGETING; GENE THERAPY; HUMANS; INTERMEDIATE FILAMENT PROTEINS; MEMBRANE GLYCOPROTEINS; MICE; MUTATION; NERVE TISSUE PROTEINS; POLYMORPHISM, GENETIC; RHODOPSIN; RNA, CATALYTIC;

EID: 9844225036     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/6.9.1415     Document Type: Article

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