Gene therapy restores vision in a canine model of childhood blindness

Nature Genetics

Volumn 28, Issue 1, 2001, Pages 92-95

  Acland, Gregory M ^a   Aguirre, Gustavo D ^a   Ray, Jharna ^a   Zhang, Qi ^a   Aleman, Tomas S ^b   Cideciyan, Artur V ^b   Pearce Kelling, Susan E ^a   Anand, Vibha ^b   Zeng, Yong ^b   Maguire, Albert M ^b   Jacobson, Samuel G ^b   Hauswirth, William W ^c   Bennett, Jean ^b  

^a Department of Population Medicine and Diagnostic Sciences   (United States)

^b UNIVERSITY OF PENNSYLVANIA   (United States)

^c UNIVERSITY OF FLORIDA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ARTICLE; BLINDNESS; CHILD; CHILDHOOD DISEASE; DOG; GENE MUTATION; GENE THERAPY; HUMAN; LEBER CONGENITAL AMAUROSIS; PHOTORECEPTOR; PIGMENT EPITHELIUM; PRIORITY JOURNAL; RETINA DEGENERATION; VISION;

ADENO-ASSOCIATED VIRUS; ANIMALIA; CANIS FAMILIARIS; RODENTIA;

EID: 0035032662     PISSN: 10614036     EISSN: None     Source Type: Journal    
DOI: 10.1038/ng0501-92     Document Type: Article

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