Knockdown of wild-type mouse rhodopsin using an AAV vectored ribozyme as part of an RNA replacement approach

Molecular Vision

Volumn 11, Issue , 2005, Pages 648-656

  Gorbatyuk, M S ^a   Pang, J J ^a   Thomas Jr , J ^a   Hauswirth, Willaim W ^a   Lewin, Alfred S ^a  

^a UNIVERSITY OF FLORIDA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; HAMMERHEAD RIBOZYME; MESSENGER RNA; OLIGONUCLEOTIDE; OPSIN; PARVOVIRUS VECTOR; RHODOPSIN; SODIUM CHLORIDE;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; AUTORADIOGRAPHY; AUTOSOMAL DOMINANT DISORDER; CELL CULTURE; CELL STRAIN HEK293; CONTROLLED STUDY; ELECTRORETINOGRAPHY; FEMALE; FLUORESCENT ANTIBODY TECHNIQUE; GENE INSERTION; GENE MUTATION; GENETIC TRANSFECTION; HUMAN; HUMAN CELL; IMMUNOCYTOCHEMISTRY; IN SITU HYBRIDIZATION; IN VITRO STUDY; MORPHOMETRICS; NONHUMAN; NUCLEOTIDE SEQUENCE; PRIORITY JOURNAL; RETINA; RETINITIS PIGMENTOSA; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; VIRAL GENE THERAPY; VIRUS CAPSID; WESTERN BLOTTING; WILD TYPE;

ANIMALS; BLOTTING, WESTERN; CELLS, CULTURED; DEPENDOVIRUS; ELECTRORETINOGRAPHY; GENE THERAPY; GENETIC VECTORS; IMMUNOHISTOCHEMISTRY; IN SITU HYBRIDIZATION; KIDNEY; MICE; MICE, INBRED C57BL; MICE, KNOCKOUT; OPSIN; RETINITIS PIGMENTOSA; REVERSE TRANSCRIPTASE POLYMERASE CHAIN REACTION; RHODOPSIN; RNA, CATALYTIC; RNA, MESSENGER; TRANSFECTION;

EID: 26244438228     PISSN: 10900535     EISSN: 10900535     Source Type: Journal    
DOI: None     Document Type: Article

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