Gene repair of an Usher syndrome causing mutation by zinc-finger nuclease mediated homologous recombination

Investigative Ophthalmology and Visual Science

Volumn 53, Issue 7, 2012, Pages 4140-4146

  Overlack, Nora ^a   Goldmann, Tobias ^a   Wolfrum, Uwe ^a   Nagel Wolfrum, Kerstin ^a  

^a JOHANNES GUTENBERG UNIVERSITY   (Germany)

Author keywords

[No Author keywords available]

Indexed keywords

ZINC FINGER NUCLEASE; DNA; ENDONUCLEASE; SIGNAL TRANSDUCING ADAPTOR PROTEIN; USH1C PROTEIN, HUMAN; ZINC FINGER PROTEIN;

ARTICLE; BIOCOMPATIBILITY; CELL CULTURE; CELL LINE; CELL VIABILITY; CONTROLLED STUDY; CYTOTOXICITY; DNA CLEAVAGE; DNA SEQUENCE; GENE; GENE MUTATION; HUMAN; HUMAN CELL; IMMUNOFLUORESCENCE MICROSCOPY; NONSENSE MUTATION; POLYMERASE CHAIN REACTION; PRIORITY JOURNAL; PROTEIN EXPRESSION; RECOMBINATION REPAIR; RETINA DISEASE; USHER SYNDROME; WESTERN BLOTTING; COMPARATIVE STUDY; DOUBLE STRANDED DNA BREAK; GENETICS; HOMOLOGOUS RECOMBINATION; METABOLISM; METHODOLOGY; PATHOLOGY; RETINA; STOP CODON; TARGETED GENE REPAIR;

ADAPTOR PROTEINS, SIGNAL TRANSDUCING; CELL LINE; CODON, NONSENSE; DNA; DNA BREAKS, DOUBLE-STRANDED; DNA CLEAVAGE; ENDONUCLEASES; HOMOLOGOUS RECOMBINATION; HUMANS; RETINA; TARGETED GENE REPAIR; USHER SYNDROMES; ZINC FINGERS;

EID: 84871899922     PISSN: 01460404     EISSN: 15525783     Source Type: Journal    
DOI: 10.1167/iovs.12-9812     Document Type: Article

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