Adeno-associated virus vector as a platform for gene therapy delivery

Nature Reviews Drug Discovery

Volumn 18, Issue 5, 2019, Pages 358-378

  Wang, Dan ^a   Tai, Phillip W L ^a   Gao, Guangping ^a  

^a UNIVERSITY OF MASSACHUSETTS MEDICAL SCHOOL   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENO ASSOCIATED VIRUS VECTOR; DNA;

ADENO ASSOCIATED VIRUS; ANALYTICAL PARAMETERS; ASSAY; BIOINFORMATICS; DNA COMPOSITION; DRUG COST; DRUG DESIGN; DRUG MANUFACTURE; GENE ADDITION; GENE DELIVERY SYSTEM; GENE EDITING; GENE EXPRESSION; GENE EXPRESSION SPECIFICITY; GENE REPLACEMENT THERAPY; GENE SILENCING; GENE THERAPY; GENETIC PARAMETERS; GENETIC PROCEDURES; HUMAN; IMMUNITY; IN VIVO GENE TRANSFER; MICROBIOLOGY; NONHUMAN; POTENCY ASSAY; PRIORITY JOURNAL; QUALITY CONTROL; REVIEW; RNA TRANSLATION; STANDARDIZATION; TRANSGENE; VECTOROLOGY; VIRUS CAPSID; VIRUS GENOME; ANIMAL; DEPENDOPARVOVIRUS; GENE TRANSFER; GENE VECTOR; GENETICS; PROCEDURES;

ANIMALS; DEPENDOVIRUS; GENE TRANSFER TECHNIQUES; GENETIC THERAPY; GENETIC VECTORS; HUMANS;

EID: 85060968995     PISSN: 14741776     EISSN: 14741784     Source Type: Journal    
DOI: 10.1038/s41573-019-0012-9     Document Type: Review

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