-
1
-
-
0028169741
-
Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain
-
Kaplitt, M.G. et al. Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain. Nature Genet. 8, 148-154 (1994).
-
(1994)
Nature Genet.
, vol.8
, pp. 148-154
-
-
Kaplitt, M.G.1
-
2
-
-
0030902462
-
Adeno-associated virus (AAV) vector antisense gene transfer in vivo decreases GABA(A) alpha1 containing receptors and increases inferior collicular seizure sensitivity
-
Xiao, X. et al. Adeno-associated virus (AAV) vector antisense gene transfer in vivo decreases GABA(A) alpha1 containing receptors and increases inferior collicular seizure sensitivity. Brain Res. 756, 76-83 (1997).
-
(1997)
Brain Res.
, vol.756
, pp. 76-83
-
-
Xiao, X.1
-
3
-
-
0033958294
-
Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy
-
Xiao, X. et al. Full functional rescue of a complete muscle (TA) in dystrophic hamsters by adeno-associated virus vector-directed gene therapy. J. Virol. 74, 1436-1442 (2000).
-
(2000)
J. Virol.
, vol.74
, pp. 1436-1442
-
-
Xiao, X.1
-
4
-
-
0029843596
-
Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector
-
Xiao, X., Li, J. & Samulski, R.J. Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector. J. Virol. 70, 8098-8108 (1996).
-
(1996)
J. Virol.
, vol.70
, pp. 8098-8108
-
-
Xiao, X.1
Li, J.2
Samulski, R.J.3
-
5
-
-
0030451214
-
Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein
-
Kessler, P.D. et al. Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein. Proc. Natl. Acad. Sci. USA 93, 14082-14087 (1996).
-
(1996)
Proc. Natl. Acad. Sci. USA
, vol.93
, pp. 14082-14087
-
-
Kessler, P.D.1
-
6
-
-
0027484584
-
Stable in vivo expression of the cystic fibrosis transmembrane conductance regulator with an adeno-associated virus vector
-
Flotte, T.R. et al. Stable in vivo expression of the cystic fibrosis transmembrane conductance regulator with an adeno-associated virus vector Proc. Natl. Acad. Sci. USA 90, 10613-10617 (1993).
-
(1993)
Proc. Natl. Acad. Sci. USA
, vol.90
, pp. 10613-10617
-
-
Flotte, T.R.1
-
7
-
-
0031875751
-
In vivo expression of therapeutic human genes for dopamine production in the caudales of MPTP-treated monkeys using an AAV vector
-
During, M.J. et al. In vivo expression of therapeutic human genes for dopamine production in the caudales of MPTP-treated monkeys using an AAV vector. Gene Ther. 5, 820-827 (1998).
-
(1998)
Gene Ther.
, vol.5
, pp. 820-827
-
-
During, M.J.1
-
8
-
-
0030997346
-
Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors
-
Snyder, R.O. et al. Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors. Nature Genet. 16, 270-276 (1997).
-
(1997)
Nature Genet.
, vol.16
, pp. 270-276
-
-
Snyder, R.O.1
-
9
-
-
0031775494
-
Adeno-associated virus as a vector for liver directed gene therapy
-
Xiao, W., Beta, S., Liu, M.M., Taxelaar, J. & Wilson, J.M. Adeno-associated virus as a vector for liver directed gene therapy. J. Virol. 72, 10222-10226 (1998).
-
(1998)
J. Virol.
, vol.72
, pp. 10222-10226
-
-
Xiao, W.1
Beta, S.2
Liu, M.M.3
Taxelaar, J.4
Wilson, J.M.5
-
10
-
-
0031880563
-
Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa
-
erratum: 4, 1081 (1998)
-
Lewin, A.S. et al. Ribozyme rescue of photoreceptor cells in a transgenic rat model of autosomal dominant retinitis pigmentosa. Nature Med. 4, 967-971 (1998); erratum: 4, 1081 (1998).
-
(1998)
Nature Med.
, vol.4
, pp. 967-971
-
-
Lewin, A.S.1
-
11
-
-
0034050904
-
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
-
Kay, M.A. et al Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector. Nature Genet. 24 257-261 (2000).
-
(2000)
Nature Genet.
, vol.24
, pp. 257-261
-
-
Kay, M.A.1
-
12
-
-
0029849257
-
Quantitative analysis of the packaging capacity of recombinant adeno-associated virus
-
Dong, J.Y., Fan, P.D. & Frizzell, R.A. Quantitative analysis of the packaging capacity of recombinant adeno-associated virus. Hum. Gene Ther. 7, 2101-2112 (1996).
-
(1996)
Hum. Gene Ther.
, vol.7
, pp. 2101-2112
-
-
Dong, J.Y.1
Fan, P.D.2
Frizzell, R.A.3
-
13
-
-
0023614188
-
Dystrophin: The protein product of the Duchenne muscular dystrophy locus
-
Hoffman, E.P., Brown, R.H., Jr. & Kunkel, L.M. Dystrophin: The protein product of the Duchenne muscular dystrophy locus. Cell 51, 919-928 (1987).
-
(1987)
Cell
, vol.51
, pp. 919-928
-
-
Hoffman, E.P.1
Brown R.H., Jr.2
Kunkel, L.M.3
-
14
-
-
17344365600
-
Dysferlin, a novel skeletal muscle gene, is mutated in Miyoshi myopathy and limb girdle muscular dystrophy
-
Liu, J. et al. Dysferlin, a novel skeletal muscle gene, is mutated in Miyoshi myopathy and limb girdle muscular dystrophy. Nature Genet. 20, 31-36 (1998).
-
(1998)
Nature Genet.
, vol.20
, pp. 31-36
-
-
Liu, J.1
-
15
-
-
0027412209
-
Expression of the cystic fibrosis transmembrane conductance regulator from a novel adeno-associated virus promoter
-
Flotte, T.R. et al. Expression of the cystic fibrosis transmembrane conductance regulator from a novel adeno-associated virus promoter. J. Biol. Chem. 268, 3781-3790 (1993).
-
(1993)
J. Biol. Chem.
, vol.268
, pp. 3781-3790
-
-
Flotte, T.R.1
-
16
-
-
0024322243
-
Organization of adeno-associated virus DNA in latently infected Detroit 6 cells
-
Kotin, R M. & Berns, K.I. Organization of adeno-associated virus DNA in latently infected Detroit 6 cells. Virology 170, 460-467 (1989).
-
(1989)
Virology
, vol.170
, pp. 460-467
-
-
Kotin, R.M.1
Berns, K.I.2
-
17
-
-
0018845021
-
Integration of the adeno-associated virus genome into cellular DNA in latently infected human Detroit 6 cells
-
Cheung, A.K., Hoggan, M.D., Hauswirth, W.W. & Berns, K.I. Integration of the adeno-associated virus genome into cellular DNA in latently infected human Detroit 6 cells. J. Virol. 33, 739-748 (1980).
-
(1980)
J. Virol.
, vol.33
, pp. 739-748
-
-
Cheung, A.K.1
Hoggan, M.D.2
Hauswirth, W.W.3
Berns, K.I.4
-
18
-
-
0023889191
-
Adeno-associated virus general transduction vectors: Analysis of proviral structures
-
McLaughlin, S.K., Collis, P., Hermonat, P.L. & Muzyczka, N. Adeno-associated virus general transduction vectors: Analysis of proviral structures. J. Virol. 62, 1963-1973 (1988).
-
(1988)
J. Virol.
, vol.62
, pp. 1963-1973
-
-
McLaughlin, S.K.1
Collis, P.2
Hermonat, P.L.3
Muzyczka, N.4
-
19
-
-
0031691257
-
Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue
-
erratum: 73, 861 (1999)
-
Duan, D. et al. Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue. J. Virol. 72, 8568-8577 (1998); erratum: 73, 861 (1999).
-
(1998)
J. Virol.
, vol.72
, pp. 8568-8577
-
-
Duan, D.1
-
20
-
-
0021265260
-
Evolution of the genes for the beta subunits of human chorionic gonadotropin and luteinizing hormone
-
Talmadge, K., Vamvakopoulos, N.C. & Fiddes, J.C. Evolution of the genes for the beta subunits of human chorionic gonadotropin and luteinizing hormone. Nature 307, 37-40 (1984).
-
(1984)
Nature
, vol.307
, pp. 37-40
-
-
Talmadge, K.1
Vamvakopoulos, N.C.2
Fiddes, J.C.3
-
21
-
-
2642642141
-
Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus
-
Xiao, X., Li, J. & Samulski, R.J. Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus. J. Virol. 72, 2224-2232 (1998).
-
(1998)
J. Virol.
, vol.72
, pp. 2224-2232
-
-
Xiao, X.1
Li, J.2
Samulski, R.J.3
-
22
-
-
0014202537
-
Selective extraction of polyoma DNA from infected mouse cultures
-
Hirt, B. Selective extraction of polyoma DNA from infected mouse cultures. J. Mol. Biol. 26, 365-369 (1967).
-
(1967)
J. Mol. Biol.
, vol.26
, pp. 365-369
-
-
Hirt, B.1
-
23
-
-
0031016643
-
A novel 165-base-pair terminal repeat sequence is the sole cis requirement for the adeno-associated virus life cycle
-
Xiao, X., Xiao, W., Li, J. & Samulski, R.J. A novel 165-base-pair terminal repeat sequence is the sole cis requirement for the adeno-associated virus life cycle. J. Virol. 71, 941-948 (1997).
-
(1997)
J. Virol.
, vol.71
, pp. 941-948
-
-
Xiao, X.1
Xiao, W.2
Li, J.3
Samulski, R.J.4
-
24
-
-
0033567129
-
Structural analysis of adeno-associated virus transduction circular intermediates
-
Duan, D., Yan, Z., Yue, Y. & Engelhardt, J.F. Structural analysis of adeno-associated virus transduction circular intermediates. Virology 261, 8-14 (1999).
-
(1999)
Virology
, vol.261
, pp. 8-14
-
-
Duan, D.1
Yan, Z.2
Yue, Y.3
Engelhardt, J.F.4
|