Protein trans-splicing as a means for viral vector-mediated in vivo gene therapy

Human Gene Therapy

Volumn 19, Issue 9, 2008, Pages 958-964

  Li, Juan ^a   Sun, Wunchang ^b   Wang, Bing ^c   Xiao, Xiao ^a   Liu, Xiang Qin ^b  

^a UNIVERSITY OF NORTH CAROLINA   (United States)

^b DALHOUSIE UNIVERSITY   (Canada)

^c UNIVERSITY OF PITTSBURGH SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; DYSTROPHIN; INTEIN; PARVOVIRUS VECTOR;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DUCHENNE MUSCULAR DYSTROPHY; GENE TARGETING; GENE THERAPY; IN VIVO STUDY; MOUSE; NONHUMAN; PROTEIN PROCESSING; RNA SPLICING; TRANS SPLICING; X CHROMOSOME LINKED MUSCULAR DYSTROPHIC MOUSE;

AMINO ACID SEQUENCE; ANIMALS; DEPENDOVIRUS; DYSTROPHIN; GENE THERAPY; GENETIC VECTORS; HUMANS; INTEINS; MICE; MICE, INBRED MDX; MOLECULAR SEQUENCE DATA; MUSCULAR DYSTROPHY, ANIMAL; MUSCULAR DYSTROPHY, DUCHENNE; PROTEIN SPLICING;

EID: 51849163544     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2008.009     Document Type: Article

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