메뉴 건너뛰기




Volumn 28, Issue 1, 2017, Pages 15-22

OneBac 2.0: Sf9 Cell Lines for Production of AAV1, AAV2, and AAV8 Vectors with Minimal Encapsidation of Foreign DNA

Author keywords

AAV; baculovirus; OneBac; packaging; Rep binding element (RBE)

Indexed keywords

ADENOVIRUS VECTOR; DNA; PROTEIN VP1;

EID: 85012977484     PISSN: 19466536     EISSN: 19466544     Source Type: Journal    
DOI: 10.1089/hgtb.2016.164     Document Type: Article
Times cited : (27)

References (23)
  • 1
    • 84925511283 scopus 로고    scopus 로고
    • Alipogene tiparvovec: A review of its use in adults with familial lipoprotein lipase deficiency
    • Scott LJ. Alipogene tiparvovec: A review of its use in adults with familial lipoprotein lipase deficiency. Drugs 2015;75:175-182.
    • (2015) Drugs , vol.75 , pp. 175-182
    • Scott, L.J.1
  • 2
    • 84911383748 scopus 로고    scopus 로고
    • Longterm safety and efficacy of factor IX gene therapy in hemophilia B
    • Nathwani AC, Reiss UM, Tuddenham EG, et al. Longterm safety and efficacy of factor IX gene therapy in hemophilia B. N Engl J Med 2014;371:1994-2004.
    • (2014) N Engl J Med , vol.371 , pp. 1994-2004
    • Nathwani, A.C.1    Reiss, U.M.2    Tuddenham, E.G.3
  • 3
    • 84878581647 scopus 로고    scopus 로고
    • Three-year follow-up after unilateral subretinal delivery of adeno-Associated virus in patients with Leber congenital amaurosis type 2
    • Testa F, Maguire AM, Rossi S, et al. Three-year follow-up after unilateral subretinal delivery of adeno-Associated virus in patients with Leber congenital amaurosis type 2. Ophthalmology 2013;120:1283-1291.
    • (2013) Ophthalmology , vol.120 , pp. 1283-1291
    • Testa, F.1    Maguire, A.M.2    Rossi, S.3
  • 4
    • 85007302654 scopus 로고    scopus 로고
    • AAV2 gene therapy readministration in three adults with congenital blindness
    • Bennett J, Ashtari M, Wellman J, et al. AAV2 gene therapy readministration in three adults with congenital blindness. Sci Transl Med 2012;4:120ra115.
    • (2012) Sci Transl Med , vol.4 , pp. 120ra115
    • Bennett, J.1    Ashtari, M.2    Wellman, J.3
  • 5
    • 0038150506 scopus 로고    scopus 로고
    • Helper virusfree, optically controllable, and two-plasmid-based production of adeno-Associated virus vectors of serotypes 1 to 6
    • Grimm D, Kay MA, Kleinschmidt JA. Helper virusfree, optically controllable, and two-plasmid-based production of adeno-Associated virus vectors of serotypes 1 to 6. Mol Ther 2003;7:839-850.
    • (2003) Mol Ther , vol.7 , pp. 839-850
    • Grimm, D.1    Kay, M.A.2    Kleinschmidt, J.A.3
  • 6
    • 2642642141 scopus 로고    scopus 로고
    • Production of high-Titer recombinant adeno-Associated virus vectors in the absence of helper adenovirus
    • Xiao X, Li J, Samulski RJ. Production of high-Titer recombinant adeno-Associated virus vectors in the absence of helper adenovirus. J Virol 1998;72:2224-2232.
    • (1998) J Virol , vol.72 , pp. 2224-2232
    • Xiao, X.1    Li, J.2    Samulski, R.J.3
  • 7
    • 0036431701 scopus 로고    scopus 로고
    • Insect cells as a factory to produce adeno-Associated virus type 2 vectors
    • Urabe M, Ding C, Kotin RM. Insect cells as a factory to produce adeno-Associated virus type 2 vectors. Hum Gene Ther 2002;13:1935-1943.
    • (2002) Hum Gene Ther , vol.13 , pp. 1935-1943
    • Urabe, M.1    Ding, C.2    Kotin, R.M.3
  • 8
    • 70449103126 scopus 로고    scopus 로고
    • A simplified baculovirus-AAV expression vector system coupled with one-step affinity purification yields hightiter rAAV stocks from insect cells
    • Smith RH, Levy JR, Kotin RM. A simplified baculovirus-AAV expression vector system coupled with one-step affinity purification yields hightiter rAAV stocks from insect cells. Mol Ther 2009;17:1888-1896.
    • (2009) Mol Ther , vol.17 , pp. 1888-1896
    • Smith, R.H.1    Levy, J.R.2    Kotin, R.M.3
  • 9
    • 65249147237 scopus 로고    scopus 로고
    • An inducible system for highly efficient production of recombinant adeno-Associated virus (rAAV) vectors in insect Sf9 cells
    • Aslanidi G, Lamb K, Zolotukhin S. An inducible system for highly efficient production of recombinant adeno-Associated virus (rAAV) vectors in insect Sf9 cells. Proc Natl Acad Sci U S A 2009;106:5059-5064.
    • (2009) Proc Natl Acad Sci U S A , vol.106 , pp. 5059-5064
    • Aslanidi, G.1    Lamb, K.2    Zolotukhin, S.3
  • 10
    • 84896368264 scopus 로고    scopus 로고
    • OneBac: Platform for scalable and high-Titer production of adeno-Associated virus serotype 1-12 vectors for gene therapy
    • Mietzsch M, Grasse S, Zurawski C, et al. OneBac: platform for scalable and high-Titer production of adeno-Associated virus serotype 1-12 vectors for gene therapy. Hum Gene Ther 2014;25:212-222.
    • (2014) Hum Gene Ther , vol.25 , pp. 212-222
    • Mietzsch, M.1    Grasse, S.2    Zurawski, C.3
  • 11
    • 84945560129 scopus 로고    scopus 로고
    • OneBac 2.0: Sf9 cell lines for production of AAV5 vectors with enhanced infectivity and minimal encapsidation of foreign DNA
    • Mietzsch M, Casteleyn V, Weger S, et al. OneBac 2.0: Sf9 cell lines for production of AAV5 vectors with enhanced infectivity and minimal encapsidation of foreign DNA. Hum Gene Ther 2015;26: 688-697.
    • (2015) Hum Gene Ther , vol.26 , pp. 688-697
    • Mietzsch, M.1    Casteleyn, V.2    Weger, S.3
  • 12
    • 42549137311 scopus 로고    scopus 로고
    • Intron splicing-mediated expression of AAV Rep and Cap genes and production of AAV vectors in insect cells
    • Chen H. Intron splicing-mediated expression of AAV Rep and Cap genes and production of AAV vectors in insect cells. Mol Ther 2008;16:924-930.
    • (2008) Mol Ther , vol.16 , pp. 924-930
    • Chen, H.1
  • 13
    • 84896730363 scopus 로고    scopus 로고
    • Differential adeno-Associated virus serotype-specific interaction patterns with synthetic heparins and other glycans
    • Mietzsch M, Broecker F, Reinhardt A, et al. Differential adeno-Associated virus serotype-specific interaction patterns with synthetic heparins and other glycans. J Virol 2014;88:2991-3003.
    • (2014) J Virol , vol.88 , pp. 2991-3003
    • Mietzsch, M.1    Broecker, F.2    Reinhardt, A.3
  • 14
    • 77953439661 scopus 로고    scopus 로고
    • A viral assembly factor promotes AAV2 capsid formation in the nucleolus
    • Sonntag F, Schmidt K, Kleinschmidt JA. A viral assembly factor promotes AAV2 capsid formation in the nucleolus. Proc Natl Acad Sci U S A 2010;107:10220-10225.
    • (2010) Proc Natl Acad Sci U S A , vol.107 , pp. 10220-10225
    • Sonntag, F.1    Schmidt, K.2    Kleinschmidt, J.A.3
  • 15
    • 0036246727 scopus 로고    scopus 로고
    • The VP1 capsid protein of adeno-Associated virus type 2 is carrying a phospholipase A2 domain required for virus infectivity
    • Girod A, Wobus CE, Zadori Z, et al. The VP1 capsid protein of adeno-Associated virus type 2 is carrying a phospholipase A2 domain required for virus infectivity. J Gen Virol 2002;83:973-978.
    • (2002) J Gen Virol , vol.83 , pp. 973-978
    • Girod, A.1    Wobus, C.E.2    Zadori, Z.3
  • 16
    • 84861998784 scopus 로고    scopus 로고
    • Intracellular transport of recombinant adeno-Associated virus vectors
    • Nonnenmacher M, Weber T. Intracellular transport of recombinant adeno-Associated virus vectors. Gene Ther 2012;19:649-658.
    • (2012) Gene Ther , vol.19 , pp. 649-658
    • Nonnenmacher, M.1    Weber, T.2
  • 17
    • 0023751447 scopus 로고
    • Synthesis of adeno-Associated virus structural proteins requires both alternative mRNA splicing and alternative initiations from a single transcript
    • Becerra SP, Koczot F, Fabisch P, et al. Synthesis of adeno-Associated virus structural proteins requires both alternative mRNA splicing and alternative initiations from a single transcript. J Virol 1988;62:2745-2754.
    • (1988) J Virol , vol.62 , pp. 2745-2754
    • Becerra, S.P.1    Koczot, F.2    Fabisch, P.3
  • 18
    • 28444473059 scopus 로고    scopus 로고
    • Successful production of pseudotyped rAAV vectors using a modified baculovirus expression system
    • Kohlbrenner E, Aslanidi G, Nash K, et al. Successful production of pseudotyped rAAV vectors using a modified baculovirus expression system. Mol Ther 2005;12:1217-1225.
    • (2005) Mol Ther , vol.12 , pp. 1217-1225
    • Kohlbrenner, E.1    Aslanidi, G.2    Nash, K.3
  • 19
    • 58149251820 scopus 로고    scopus 로고
    • Undetectable transcription of cap in a clinical AAV vector: Implications for preformed capsid in immune responses
    • Hauck B, Murphy SL, Smith PH, et al. Undetectable transcription of cap in a clinical AAV vector: implications for preformed capsid in immune responses. Mol Ther 2009;17:144-152.
    • (2009) Mol Ther , vol.17 , pp. 144-152
    • Hauck, B.1    Murphy, S.L.2    Smith, P.H.3
  • 20
    • 84883020987 scopus 로고    scopus 로고
    • Generation and characterization of adeno-Associated virus producer cell lines for research and preclinical vector production
    • Martin J, Frederick A, Luo Y, et al. Generation and characterization of adeno-Associated virus producer cell lines for research and preclinical vector production. Hum Gene Ther Methods 2013;24:253-269.
    • (2013) Hum Gene Ther Methods , vol.24 , pp. 253-269
    • Martin, J.1    Frederick, A.2    Luo, Y.3
  • 21
    • 84959337169 scopus 로고    scopus 로고
    • Advanced characterization of DNA molecules in rAAV vector preparations by single-stranded virus next-generation sequencing
    • Lecomte E, Tournaire B, Cogne B, et al. Advanced characterization of DNA molecules in rAAV vector preparations by single-stranded virus next-generation sequencing. Mol Ther Nucleic Acids 2015;4:e260.
    • (2015) Mol Ther Nucleic Acids , vol.4 , pp. e260
    • Lecomte, E.1    Tournaire, B.2    Cogne, B.3
  • 22
    • 0344406980 scopus 로고    scopus 로고
    • Packaging of human chromosome 19-specific adeno-Associated virus (AAV) integration sites in AAV virions during AAV wild-Type and recombinant AAV vector production
    • Hüser D, Weger S, Heilbronn R. Packaging of human chromosome 19-specific adeno-Associated virus (AAV) integration sites in AAV virions during AAV wild-Type and recombinant AAV vector production. J Virol 2003;77:4881-4887.
    • (2003) J Virol , vol.77 , pp. 4881-4887
    • Hüser, D.1    Weger, S.2    Heilbronn, R.3
  • 23
    • 84906058160 scopus 로고    scopus 로고
    • A draft genome assembly of the army worm Spodoptera frugiperda
    • Kakumani PK, Malhotra P, Mukherjee SK, et al. A draft genome assembly of the army worm, Spodoptera frugiperda. Genomics 2014;104:134-143.
    • (2014) Genomics , vol.104 , pp. 134-143
    • Kakumani, P.K.1    Malhotra, P.2    Mukherjee, S.K.3


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.