Efficient in vivo gene expression by trans-splicing adeno-associated viral vectors

Nature Biotechnology

Volumn 23, Issue 11, 2005, Pages 1435-1439

  Lai, Yi ^a   Yue, Yongping ^a   Liu, Mingju ^a   Ghosh, Arkasubhra ^a   Engelhardt, John F ^b   Chamberlain, Jeffrey S ^c   Duan, Dongsheng ^a  

^a University of Missouri   (United States)

^b UNIVERSITY OF IOWA   (United States)

^c UNIVERSITY OF WASHINGTON SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

MATHEMATICAL MODELS; PROTEINS; VECTORS;

AAV VECTORS; PACKAGING CAPACITY;

GENES;

DYSTROPHIN; PARVOVIRUS VECTOR; STRUCTURAL PROTEIN;

ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; DUCHENNE MUSCULAR DYSTROPHY; EXON; EXPRESSION VECTOR; GENE EXPRESSION; GENETIC TRANSCRIPTION; INTRON; MALE; MOUSE; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL; PROTEIN EXPRESSION; PROTEIN STRUCTURE; SKELETAL MUSCLE; TRANS SPLICING;

ANIMALS; CELL LINE; DEPENDOVIRUS; DYSTROPHIN; EXONS; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; INTRONS; MALE; MICE; MICE, INBRED MDX; MODELS, STATISTICAL; MUSCLE, SKELETAL; MUSCLES; PHENOTYPE; RNA SPLICING; RNA, MESSENGER; TRANS-SPLICING; TRANSCRIPTION, GENETIC;

ADENO-ASSOCIATED VIRUS; ANIMALIA; PARVOVIRUS;

EID: 27944479711     PISSN: 10870156     EISSN: 15461696     Source Type: Journal    
DOI: 10.1038/nbt1153     Document Type: Article

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