Emerging Gene Therapies for Genetic Hearing Loss

JARO - Journal of the Association for Research in Otolaryngology

Volumn 18, Issue 5, 2017, Pages 649-670

  Ahmed, Hena ^a   Shubina Oleinik, Olga ^a   Holt, Jeffrey R ^a  

^a BOSTON CHILDREN S HOSPITAL   (United States)

Author keywords

cochlea; gene therapy; genetic deafness; hair cell; inner ear; spiral ganglion neuron; vestibular; viral vectors

Indexed keywords

CONNEXIN 26; LENTIVIRUS VECTOR; POTASSIUM CHANNEL KCNE1; POTASSIUM CHANNEL KCNQ1; VESICULAR GLUTAMATE TRANSPORTER 3; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ADENOVIRIDAE; BLOOD BRAIN BARRIER; CELL COMMUNICATION; CELL FUNCTION; EXON; EXOSOME; GENE; GENE EDITING; GENE MUTATION; GENE REPLACEMENT THERAPY; GENE SILENCING; GENE TARGETING; GENE THERAPY; GENETIC DISORDER; GUINEA PIG; HAIR CELL; HEARING IMPAIRMENT; HUMAN; IN VITRO STUDY; INDEL MUTATION; INNER EAR; NERVE CELL; NONHUMAN; NONVIRAL GENE THERAPY; PRIORITY JOURNAL; PROMOTER REGION; REVIEW; RNA TRANSLATION; SPIRAL GANGLION; STRIA VASCULARIS; SUSTENTACULAR CELL; USH1C GENE; USH3A GENE; ANIMAL; GENE VECTOR; GENETICS; PROCEDURES; TRANSLATIONAL RESEARCH; TRENDS;

ANIMALS; GENETIC THERAPY; GENETIC VECTORS; HEARING LOSS; HUMANS; TRANSLATIONAL MEDICAL RESEARCH;

EID: 85027531668     PISSN: 15253961     EISSN: 14387573     Source Type: Journal    
DOI: 10.1007/s10162-017-0634-8     Document Type: Review

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