Dual adeno-associated virus vectors result in efficient in vitro and in vivo expression of an oversized gene, MYO7A

Human Gene Therapy Methods

Volumn 25, Issue 2, 2014, Pages 166-177

  Dyka, Frank M ^a   Boye, Sanford L ^a   Chiodo, Vince A ^a   Hauswirth, William W ^a   Boye, Shannon E ^a  

^a UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; FRAGMENTED ADENO ASSOCIATED VIRUS VECTOR; MESSENGER RNA; MYOSIN VIIA; PARVOVIRUS VECTOR; UNCLASSIFIED DRUG; VIRUS VECTOR; MYOSIN; RECOMBINANT PROTEIN;

ANIMAL EXPERIMENT; ARTICLE; CELL STRAIN HEK293; CLONE; CONTROLLED STUDY; GENE EXPRESSION; GENE LOCATION; GENE PRODUCT; GENE SEQUENCE; GENE TARGETING; HUMAN; HUMAN CELL; HYBRID GENE; IN VITRO STUDY; IN VIVO STUDY; INVERTED TERMINAL REPEAT; MOUSE; NONHUMAN; NUCLEOTIDE BINDING SITE; POLYADENYLATION; PRIORITY JOURNAL; PROMOTER REGION; TRANS SPLICING; USHER SYNDROME; VIRAL GENE DELIVERY SYSTEM; ANIMAL; BIOSYNTHESIS; C57BL MOUSE; DEPENDOPARVOVIRUS; GENE EXPRESSION REGULATION; GENE VECTOR; GENETICS; HEK293 CELL LINE; IMMUNOHISTOCHEMISTRY; METABOLISM; MOLECULAR CLONING; PATHOLOGY; POLYACRYLAMIDE GEL ELECTROPHORESIS; RETINA; RNA SPLICING; SEROTYPING;

ANIMALS; CLONING, MOLECULAR; DEPENDOVIRUS; ELECTROPHORESIS, POLYACRYLAMIDE GEL; GENE EXPRESSION REGULATION; GENETIC VECTORS; HEK293 CELLS; HUMANS; IMMUNOHISTOCHEMISTRY; MICE; MICE, INBRED C57BL; MYOSINS; RECOMBINANT PROTEINS; RETINA; RNA SPLICING; SEROTYPING;

EID: 84898722805     PISSN: 19466536     EISSN: 19466544     Source Type: Journal    
DOI: 10.1089/hgtb.2013.212     Document Type: Article

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