Triple trans-splicing adeno-associated virus vectors capable of transferring the coding sequence for full-length dystrophin protein into dystrophic mice

Human Gene Therapy

Volumn 25, Issue 2, 2014, Pages 98-108

  Koo, Taeyoung ^a,b   Popplewell, Linda ^a   Athanasopoulos, Takis ^a,c   Dickson, George ^a  

^a UNIVERSITY OF LONDON   (United Kingdom)

^b UNIVERSITY OF OXFORD   (United Kingdom)

^c UNIVERSITY OF WOLVERHAMPTON   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

ANIMALS; BASE SEQUENCE; DEPENDOVIRUS; DYSTROPHIN; GENE AMPLIFICATION; GENE EXPRESSION; GENE ORDER; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; MALE; MICE; MICE, INBRED MDX; MOLECULAR SEQUENCE DATA; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, ANIMAL; OPEN READING FRAMES; SEQUENCE ALIGNMENT; TRANS-SPLICING; TRANSCRIPTION, GENETIC;

EID: 84893698363     PISSN: 10430342     EISSN: 15577422     Source Type: Journal    
DOI: 10.1089/hum.2013.164     Document Type: Article

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