Impact of gene editing on the study of cystic fibrosis

Human Genetics

Volumn 135, Issue 9, 2016, Pages 983-992

  Harrison, Patrick T ^a   Sanz, David J ^a   Hollywood, Jennifer A ^a,b  

^a UNIVERSITY COLLEGE CORK   (Ireland)

^b UNIVERSITY OF AUCKLAND   (New Zealand)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; DOXYCYCLINE; GENOMIC DNA; GENOMIC RNA; IVACAFTOR; LENTIVIRUS VECTOR; NUCLEASE; PEPTIDE; RNA; ZINC FINGER NUCLEASE;

CELL DIFFERENTIATION; CLINICAL TRIAL (TOPIC); CYSTIC FIBROSIS; DISEASE SEVERITY; DNA TEMPLATE; DOUBLE STRANDED DNA BREAK; DRUG FORMULATION; GENE EXPRESSION; GENE TARGETING; GENETIC MODEL; GENETIC VARIABILITY; GENOME-WIDE ASSOCIATION STUDY; HUMAN; INTESTINAL STEM CELL; LUNG DISEASE; LUNG FIBROSIS; LUNG FUNCTION; MODIFIER GENE; NONHUMAN; PRIORITY JOURNAL; RABBIT; REVIEW; RNA EDITING; VIRAL GENE DELIVERY SYSTEM; ANIMAL; BIOLOGICAL MODEL; GENE EDITING; GENETICS;

ANIMALS; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; GENE EDITING; HUMANS; MODELS, GENETIC;

EID: 84975282868     PISSN: 03406717     EISSN: 14321203     Source Type: Journal    
DOI: 10.1007/s00439-016-1693-3     Document Type: Review

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