Expression of ΔF508 CFTR in normal mouse lung after site-specific modification of CFTR sequences by SFHR

Gene Therapy

Volumn 8, Issue 12, 2001, Pages 961-965

  Goncz, K K ^a   Colosimo, A ^a,b   Dallapiccola, B ^c   Gagne L ^d   Hong, K ^e   Novelli, G ^f   Papahadjopoulos, D ^e   Sawa, T ^g   Schreier, H ^h   Wiener Kronish, J ^g   Xu, Z ^g   Gruenert, D C ^a  

^a UNIVERSITY OF VERMONT COLLEGE OF MEDICINE   (United States)

^b UNIVERSITY OF CHIETI   (Italy)

^c SAPIENZA UNIVERSITY OF ROME   (Italy)

^d UNIVERSITY OF CALIFORNIA   (United States)

^e CALIFORNIA PACIFIC MEDICAL CENTER   (United States)

^f UNIVERSITY OF ROME TOR VERGATA   (Italy)

^g UNIVERSITY OF CALIFORNIA   (United States)

^h Vectron Therapeutics AG   (Germany)

Author keywords

Cystic fibrosis; DNA delivery vehicles; Gene targeting; Gene therapy

Indexed keywords

COMPLEMENTARY DNA; DNA; DNA FRAGMENT; DRUG VEHICLE; MESSENGER RNA; TRANSMEMBRANE CONDUCTANCE REGULATOR; CATION EXCHANGE RESIN; DIDODECYLDIMETHYLAMMONIUM; LIPID; LIPOFECTAMINE; LIPOSOME; QUATERNARY AMMONIUM DERIVATIVE; VIROSOME;

AIRWAY; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; CONTROLLED STUDY; CYSTIC FIBROSIS; DEGRADATION; DNA MODIFICATION; DNA VECTOR; EPITHELIUM CELL; EXON; GENE AMPLIFICATION; GENE DELETION; GENE EXPRESSION; GENE INSERTION; GENE MUTATION; GENE SEQUENCE; GENE TARGETING; GENE THERAPY; GENETIC DISORDER; HUMAN; HUMAN CELL; IN VITRO STUDY; IN VIVO STUDY; LUNG; MOUSE; NONHUMAN; POLYMERASE CHAIN REACTION; PRIORITY JOURNAL; SEQUENCE HOMOLOGY; SITE DIRECTED MUTAGENESIS; SOMATIC CELL; ANIMAL; GENE VECTOR; GENETIC TRANSFECTION; GENETICS; METABOLISM; METHODOLOGY; TRANSGENIC MOUSE;

ANIMALS; CATION EXCHANGE RESINS; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; GENE DELETION; GENE EXPRESSION; GENE THERAPY; GENETIC VECTORS; LIPIDS; LIPOSOMES; LUNG; MICE; MICE, TRANSGENIC; QUATERNARY AMMONIUM COMPOUNDS; RNA, MESSENGER; TRANSFECTION; VIROSOMES;

EID: 0034743499     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3301476     Document Type: Article

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