Novel siRNA delivery strategy: A new "strand" in CNS translational medicine?

Cellular and Molecular Life Sciences

Volumn 71, Issue 1, 2014, Pages 1-20

  Gherardini, Lisa ^a   Bardi, Giuseppe ^b   Gennaro, Mariangela ^a   Pizzorusso, Tommaso ^a,c  

^a CNR   (Italy)

^b ISTITUTO ITALIANO DI TECNOLOGIA   (Italy)

^c UNIVERSITY OF FLORENCE   (Italy)

Author keywords

Gene therapy; Nanoparticles; Neurodegeneration; RNA interference

Indexed keywords

ADENOVIRUS VECTOR; AGN 211745; LENTIVIRUS VECTOR; NANOPARTICLE; PARVOVIRUS VECTOR; PEPTIDE; PF 04523655; SMALL INTERFERING RNA; SYL 1001; UNCLASSIFIED DRUG;

ALZHEIMER DISEASE; AMYOTROPHIC LATERAL SCLEROSIS; BLOOD BRAIN BARRIER; CANCER THERAPY; CENTRAL NERVOUS SYSTEM; CEREBROVASCULAR ACCIDENT; DRUG ADMINISTRATION ROUTE; DRUG DELIVERY SYSTEM; DRY EYE; ENZYMATIC DEGRADATION; EYE DISCOMFORT; GLIOBLASTOMA; HUMAN; HUNTINGTON CHOREA; NEUROPATHIC PAIN; NONHUMAN; PARKINSON DISEASE; RETINA MACULA AGE RELATED DEGENERATION; RETINOBLASTOMA; REVIEW; RNA INTERFERENCE; SCHIZOPHRENIA; SUBRETINAL NEOVASCULARIZATION; TRANSLATIONAL RESEARCH; VISCERAL PAIN;

EID: 84891878822     PISSN: 1420682X     EISSN: 14209071     Source Type: Journal    
DOI: 10.1007/s00018-013-1310-8     Document Type: Review

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