New pharmacological approaches for cystic fibrosis: Promises, progress, pitfalls

Pharmacology and Therapeutics

Volumn 145, Issue , 2015, Pages 19-34

  Bell, Scott C ^a,b   De Boeck, Kris ^c   Amaral, Margarida D ^d  

^a THE PRINCE CHARLES HOSPITAL   (Australia)

^b Queensland Children's Medical Research Institute   (Australia)

^c UNIVERSITY OF LEUVEN   (Belgium)

^d UNIVERSITY OF LISBON   (Portugal)

Author keywords

CFTR2; Correctors; Cystic fibrosis; Cystic fibrosis transmembrane conductance regulator protein; Potentiators; Trial end points

Indexed keywords

ATALUREN; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; GENTAMICIN; IVACAFTOR; LUMACAFTOR;

ARTICLE; CELL THERAPY; CLINICAL ASSESSMENT; CLINICAL DECISION MAKING; CLINICAL PRACTICE; CLINICAL TRIAL (TOPIC); CYSTIC FIBROSIS; DISEASE COURSE; DISEASE SEVERITY; DRUG EFFICACY; GENE DELETION; GENE INSERTION; GENE THERAPY; HISTORY; HUMAN; NONHUMAN; NONSENSE MUTATION; PHARMACEUTICAL CARE; PREVALENCE; PROTEIN EXPRESSION; PROTEIN PROCESSING; ANIMAL; GENETICS; METABOLISM; MUTATION;

ANIMALS; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; HUMANS; MUTATION;

EID: 84918819788     PISSN: 01637258     EISSN: 1879016X     Source Type: Journal    
DOI: 10.1016/j.pharmthera.2014.06.005     Document Type: Review

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