Gene therapy of storage disorders by retroviral and lentiviral vectors

Human Gene Therapy

Volumn 16, Issue 10, 2005, Pages 1133-1142

  Biffi, Alessandra ^a   Naldini, Luigi ^a  

^a VITA SALUTE SAN RAFFAELE UNIVERSITY   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

LENTIVIRUS VECTOR; LYSOSOME ENZYME; RETROVIRUS VECTOR; VIRUS VECTOR;

CELL DIFFERENTIATION; CENTRAL NERVOUS SYSTEM; ENZYME REPLACEMENT; FABRY DISEASE; GENE THERAPY; GENE TRANSFER; GENETIC TRANSDUCTION; GLOBOID CELL LEUKODYSTROPHY; GLYCOGEN STORAGE DISEASE TYPE 2; GM1 GANGLIOSIDOSIS; HEMATOPOIETIC STEM CELL; LYSOSOME STORAGE DISEASE; METACHROMATIC LEUKODYSTROPHY; NERVE CELL; NEURAL STEM CELL; NONHUMAN; REVIEW; RISK BENEFIT ANALYSIS; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY;

ANIMALS; GENE THERAPY; GENETIC VECTORS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; LENTIVIRUS; LYSOSOMAL STORAGE DISEASES; NEURONS; TRANSDUCTION, GENETIC;

LENTIVIRUS;

EID: 26644436945     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2005.16.1133     Document Type: Review

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