Treatment of lysosomal storage disease in MPS VII mice using a recombinant adeno-associated virus

Gene Therapy

Volumn 5, Issue 12, 1998, Pages 1642-1649

  Watson, G L ^a   Sayles, J N ^b   Chen, C ^b   Elliger, S S ^b   Elliger, C A ^b   Raju, N R ^b   Kurtzman, G J ^b   Podsakoff, G M ^b  

^a CHILDREN S HOSPITAL OAKLAND RESEARCH INSTITUTE   (United States)

^b NONE

Author keywords

Adeno associated virus; Gene therapy; Lysosomal storage disease; Mucopolysaccharidosis; glucuronidase

Indexed keywords

BETA GLUCURONIDASE; COMPLEMENTARY DNA; GLYCOSAMINOGLYCAN;

ADENOVIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL TYPE; CONTROLLED STUDY; ENZYME ACTIVITY; ENZYME DEFICIENCY; EXPRESSION VECTOR; GENE THERAPY; INTRAMUSCULAR DRUG ADMINISTRATION; INTRAVENOUS DRUG ADMINISTRATION; LIVER; MOUSE; MUCOPOLYSACCHARIDOSIS TYPE 7; NONHUMAN; PHENOTYPE; PRIORITY JOURNAL;

ADENO-ASSOCIATED VIRUS; ADENOVIRIDAE; ANIMALIA;

EID: 0032444325     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3300775     Document Type: Article

References (11)

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