Reversal of pathology in the entire brain of mucopolysaccharidosis type VII mice after lentivirus-mediated gene transfer

Human Gene Therapy

Volumn 11, Issue 8, 2000, Pages 1139-1150

  Bosch, Assumpciö ^a   Perret, Emmanuelle ^b   Desmaris, Nathalie ^a   Trono, Didier ^c   Heard, Jean Michel ^a,b  

^a CNRS   (France)

^b INSTITUT PASTEUR   (France)

^c UNIVERSITY OF GENEVA MEDICAL SCHOOL   (Switzerland)

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLUCURONIDASE;

ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; ENZYME ACTIVITY; GENE EXPRESSION; GENE TRANSFER; HUMAN IMMUNODEFICIENCY VIRUS 1; LENTIVIRINAE; LYSOSOME STORAGE DISEASE; MOUSE; MUCOPOLYSACCHARIDOSIS; NONHUMAN; REPORTER GENE; TREATMENT OUTCOME;

ANIMALS; BETA-GALACTOSIDASE; BETA-N-ACETYLHEXOSAMINIDASE; BRAIN; DISEASE MODELS, ANIMAL; DOSE-RESPONSE RELATIONSHIP, DRUG; GENE TRANSFER TECHNIQUES; GLUCURONIDASE; HIV; IN SITU HYBRIDIZATION; LENTIVIRUS; MICE; MUCOPOLYSACCHARIDOSIS VII; PLASMIDS; POLYMERASE CHAIN REACTION; TIME FACTORS; TISSUE DISTRIBUTION;

EID: 0034690714     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/10430340050015194     Document Type: Article

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