Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning

Science

Volumn 296, Issue 5577, 2002, Pages 2410-2413

  Aiuti, Alessandro ^a   Slavin, Shimon ^a   Aker, Memet ^a   Ficara, Francesca ^a   Deola, Sara ^a   Mortellaro, Alessandra ^a   Morecki, Shoshana ^a   Andolfi, Grazia ^a   Tabucchi, Antonella ^a   Carlucci, Filippo ^a   Marinello, Enrico ^a   Cattaneo, Federica ^a   Vai, Sergio ^a   Servida, Paolo ^a   Miniero, Roberto ^a   Roncarolo, Maria Grazia ^a   Bordignon, Claudio ^a  

^a SAN RAFFAELE SCIENTIFIC INSTITUTE   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

ACCIDENT PREVENTION; CELLS; ENZYMES; GENES; HOUSES; IMMUNOLOGY; TOXIC MATERIALS;

GENE THERAPY;

GENETIC ENGINEERING;

ADENOSINE DEAMINASE;

GENE; GENETICS; IMMUNE RESPONSE;

ARTICLE; CASE REPORT; CELL DIFFERENTIATION; COMBINED IMMUNODEFICIENCY; ENZYME REPLACEMENT; GENE THERAPY; GENE TRANSFER; HEMATOPOIETIC STEM CELL; HUMAN; LYMPHOCYTE COUNT; POLYMERASE CHAIN REACTION; PRIORITY JOURNAL; QUANTITATIVE ASSAY;

ADENOSINE DEAMINASE; ANIMALS; B-LYMPHOCYTES; BONE MARROW TRANSPLANTATION; CELL DIFFERENTIATION; CHILD, PRESCHOOL; GENE THERAPY; GENETIC VECTORS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMATOPOIETIC STEM CELLS; HUMANS; IMMUNOGLOBULINS; INFANT; LEUKOCYTES; LEUKOPOIESIS; LYMPHOCYTE ACTIVATION; MICE; MICE, SCID; RETROVIRIDAE; SEVERE COMBINED IMMUNODEFICIENCY; T-LYMPHOCYTES; TRANSDUCTION, GENETIC; TRANSPLANTATION CONDITIONING;

ADA;

EID: 0037189401     PISSN: 00368075     EISSN: None     Source Type: Journal    
DOI: 10.1126/science.1070104     Document Type: Article

References (27)