Transplantation of umbilical-cord blood in babies with infantile Krabbe's disease

New England Journal of Medicine

Volumn 352, Issue 20, 2005, Pages 2069-2081

  Escolar, Maria L ^a   Poe, Michele D ^a   Provenzale, James M ^b   Richards, Karen C ^b   Allison, June ^b   Wood, Susan ^b   Wenger, David A ^c   Pietryga, Daniel ^d   Wall, Donna ^e   Champagne, Martin ^f   Morse, Richard ^b   Krivit, William ^g   Kurtzberg, Joanne ^b  

^a UNIVERSITY OF NORTH CAROLINA   (United States)

^b DUKE UNIVERSITY MEDICAL CENTER   (United States)

^c THOMAS JEFFERSON UNIVERSITY   (United States)

^d HELEN DEVOS CHILDREN S HOSPITAL   (United States)

^e TEXAS TRANSPLANT INSTITUTE   (United States)

^f UNIVERSITY OF MONTREAL   (Canada)

^g UNIVERSITY OF MINNESOTA MEDICAL SCHOOL   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BUSULFAN; CYCLOPHOSPHAMIDE; GALACTOSYLCERAMIDASE; THYMOCYTE ANTIBODY;

ADAPTIVE BEHAVIOR; ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION; ARTICLE; CLINICAL ARTICLE; COGNITIVE DEVELOPMENT; CONTROLLED STUDY; DISEASE COURSE; ELECTROENCEPHALOGRAPHY; ENZYME BLOOD LEVEL; EVOKED AUDITORY RESPONSE; EVOKED VISUAL RESPONSE; FEMALE; FOLLOW UP; GLOBOID CELL LEUKODYSTROPHY; GRAFT VERSUS HOST REACTION; HUMAN; INFANT; KAPLAN MEIER METHOD; LANGUAGE DEVELOPMENT; MALE; MOTOR DEVELOPMENT; MYELINATION; MYELOABLATIVE CONDITIONING; NERVE CELL DIFFERENTIATION; NERVE CONDUCTION; NEWBORN; NUCLEAR MAGNETIC RESONANCE IMAGING; PRIORITY JOURNAL; SURVIVAL RATE; TREATMENT OUTCOME; UMBILICAL CORD BLOOD;

BRAIN; CHILD DEVELOPMENT; CORD BLOOD STEM CELL TRANSPLANTATION; DISEASE PROGRESSION; ELECTROENCEPHALOGRAPHY; EVOKED POTENTIALS; FEMALE; FETAL BLOOD; GALACTOSYLCERAMIDASE; GRAFT SURVIVAL; GROWTH; HISTOCOMPATIBILITY TESTING; HUMANS; INFANT; INFANT BEHAVIOR; INFANT, NEWBORN; LEUKODYSTROPHY, GLOBOID CELL; LONGITUDINAL STUDIES; MALE; MOTOR SKILLS; MOTOR SKILLS DISORDERS; NEURAL CONDUCTION; SURVIVAL ANALYSIS; TRANSPLANTATION CONDITIONING; TREATMENT OUTCOME;

EID: 20844453744     PISSN: 00284793     EISSN: None     Source Type: Journal    
DOI: 10.1056/NEJMoa042604     Document Type: Article

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