Bone marrow stem cell gene therapy of arylsulfatase A-deficient mice, using an arylsulfatase a mutant that is hypersecreted from retrovirally transduced donor-type cells

Human Gene Therapy

Volumn 12, Issue 9, 2001, Pages 1021-1033

  Matzner, U ^a   Schestag, F ^a   Hartmann, D ^b   Lullmann Rauch R ^b   D'Hooge, R ^c   De Deyn, P P ^c   Gieselmann, V ^a  

^a UNIVERSITY OF BONN   (Germany)

^b UNIVERSITY OF KIEL   (Germany)

^c UNIVERSITY OF ANTWERP   (Belgium)

Author keywords

[No Author keywords available]

Indexed keywords

CEREBROSIDE SULFATASE; COMPLEMENTARY DNA; MANNOSE 6 PHOSPHATE; SOMATOMEDIN B RECEPTOR; SULFATIDE; VIRUS VECTOR;

ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; BONE MARROW TRANSPLANTATION; ENDOCYTOSIS; ENZYME GLYCOSYLATION; ENZYME RELEASE; GAIT; GENE EXPRESSION; GENE THERAPY; HEMATOPOIETIC STEM CELL; HISTOPATHOLOGY; LYSOSOME STORAGE DISEASE; METACHROMATIC LEUKODYSTROPHY; MOUSE; NEUROLOGIC DISEASE; NONHUMAN; PROTEIN EXPRESSION; TISSUE LEVEL; TRANSGENE; TREATMENT OUTCOME;

3T3 CELLS; ANIMALS; BEHAVIOR, ANIMAL; BONE MARROW CELLS; BONE MARROW TRANSPLANTATION; CELL LINE; CEREBROSIDE-SULFATASE; ENZYME STABILITY; FEMALE; GENE TARGETING; GENE THERAPY; GENETIC VECTORS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMANS; LYSOSOMAL STORAGE DISEASES; MICE; MICE, KNOCKOUT; MUTATION; RETROVIRIDAE; TRANSDUCTION, GENETIC;

EID: 0034928447     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/104303401750214258     Document Type: Article

References (41)

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