Decreased lysosomal storage in the adult MPS VII mouse brain in the vicinity of grafts of retroviral vector-corrected fibroblasts secreting high levels of β-glucuronidase

Nature Medicine

Volumn 3, Issue 7, 1997, Pages 771-774

  Taylor, Rosanne M ^a,b   Wolfe, John H ^a  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

^b UNIVERSITY OF SYDNEY   (Australia)

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLUCURONIDASE;

ANIMAL TISSUE; ARTICLE; FIBROBLAST; GENE TRANSFER; LYSOSOME STORAGE DISEASE; MENTAL DEFICIENCY; MOUSE; MUCOPOLYSACCHARIDOSIS; MUCOPOLYSACCHARIDOSIS TYPE 7; NONHUMAN; PRIORITY JOURNAL; RETROVIRUS;

ANIMALS; BRAIN; CELL LINE; CELL TRANSPLANTATION; CELLS, CULTURED; CEREBRAL CORTEX; DISEASE MODELS, ANIMAL; FIBROBLASTS; FIBRONECTINS; GENE THERAPY; GENETIC VECTORS; GLUCURONIDASE; HUMANS; LYSOSOMES; MICE; MICE, INBRED C57BL; MUCOPOLYSACCHARIDOSIS VII; NEUROGLIA; NEURONS; RETROVIRIDAE; THALAMUS;

ANIMALIA; MURINAE; UNIDENTIFIED RETROVIRUS;

EID: 0030854815     PISSN: 10788956     EISSN: None     Source Type: Journal    
DOI: 10.1038/nm0797-771     Document Type: Article

References (19)

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