Overcoming cellular barriers for RNA therapeutics

Nature Biotechnology

Volumn 35, Issue 3, 2017, Pages 222-229

  Dowdy, Steven F ^a  

^a UNIVERSITY OF CALIFORNIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

GENE THERAPY; GENES; LIPID BILAYERS; NEURODEGENERATIVE DISEASES; NUCLEIC ACIDS; OLIGONUCLEOTIDES;

ALZHEIMER'S DISEASE; ANTISENSE OLIGONUCLEOTIDES; CELLULAR BARRIERS; GENE PRODUCTS; LARGE PARTS; PANDEMIC INFLUENZA; RNA THERAPEUTICS; THERAPEUTIC PARADIGMS;

RNA;

ANTISENSE OLIGONUCLEOTIDE; APTAMER; DOUBLE STRANDED RNA; GUIDE RNA; MESSENGER RNA; MICRORNA; RNA; SINGLE STRANDED RNA; SMALL INTERFERING RNA; SYNTHETIC RNA; UNCLASSIFIED DRUG; NANOCAPSULE;

BIOCHEMISTRY; CELL INVASION; CRISPR CAS SYSTEM; GENE PRODUCT; GENE TARGETING; GENE THERAPY; HUMAN; LIPID BILAYER; MOLECULAR EVOLUTION; MOLECULAR MEDICINE; NONHUMAN; PHASE 3 CLINICAL TRIAL (TOPIC); PRIORITY JOURNAL; REVIEW; ANIMAL; CELL MEMBRANE; CHEMISTRY; METABOLISM; MOLECULARLY TARGETED THERAPY; PROCEDURES; RNA INTERFERENCE; RNAI THERAPEUTICS; ULTRASTRUCTURE;

ANIMALS; CELL MEMBRANE; HUMANS; MOLECULAR TARGETED THERAPY; NANOCAPSULES; RNA; RNA INTERFERENCE; RNAI THERAPEUTICS;

EID: 85014736062     PISSN: 10870156     EISSN: 15461696     Source Type: Journal    
DOI: 10.1038/nbt.3802     Document Type: Review

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