Gene therapy for cystic fibrosis

Clinical Reviews in Allergy and Immunology

Volumn 35, Issue 3, 2008, Pages 164-178

  Mueller, Christian ^a   Flotte, Terence R ^a  

^a UNIVERSITY OF MASSACHUSETTS MEDICAL SCHOOL   (United States)

Author keywords

AAV; Ad; CF; Cystic fibrosis; Gene therapy; Immune responses; Liposomes; Non viral

Indexed keywords

ADENOVIRUS VECTOR; CHLORIDE ION; EPITHELIAL SODIUM CHANNEL; GL 67; LEUKOCYTE ELASTASE; LIPOSOME; LYSOPHOSPHATIDYLCHOLINE; MACROGOL; PLACEBO; POLYAMIDOAMINE; POLYETHYLENEIMINE; POLYMER; TRANSMEMBRANE CONDUCTANCE REGULATOR; UNCLASSIFIED DRUG;

BRONCHITIS; CHROMOSOME 7; CLINICAL TRIAL; CYSTIC FIBROSIS; DRUG DOSE ESCALATION; FEVER; FORCED EXPIRATORY VOLUME; GENE EXPRESSION; GENE MUTATION; GENE TARGETING; GENE THERAPY; GENE TRANSFER; GENE VECTOR; GENETIC PREDISPOSITION; HUMAN; HUMORAL IMMUNITY; INNATE IMMUNITY; ION TRANSPORT; LUNG FUNCTION; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; PSEUDOMONAS AERUGINOSA; REVIEW; STAPHYLOCOCCUS AUREUS; VIRAL GENE DELIVERY SYSTEM; VIRUS GENE; ANIMAL; CELLULAR IMMUNITY; GENETICS; IMMUNOLOGY; METABOLISM; METHODOLOGY; PROTEIN TRANSPORT; RECESSIVE GENE; SIGNAL TRANSDUCTION; SITE DIRECTED MUTAGENESIS; STEM CELL; TARGETED GENE REPAIR;

ANIMALS; CYSTIC FIBROSIS; CYSTIC FIBROSIS TRANSMEMBRANE CONDUCTANCE REGULATOR; GENE THERAPY; GENES, RECESSIVE; GENETIC PREDISPOSITION TO DISEASE; GENETIC VECTORS; HUMANS; IMMUNITY, CELLULAR; MUTAGENESIS, SITE-DIRECTED; PROTEIN TRANSPORT; SIGNAL TRANSDUCTION; STEM CELLS; TARGETED GENE REPAIR;

EID: 59449104014     PISSN: 10800549     EISSN: None     Source Type: Journal    
DOI: 10.1007/s12016-008-8080-3     Document Type: Review

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