Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus

Proceedings of the National Academy of Sciences of the United States of America

Volumn 94, Issue 13, 1997, Pages 6916-6921

  Flannery, John G ^a   Zolotukhin, Sergei ^b   Vaquero, M Isabel ^b   LaVail, Matthew M ^c   Muzyczka, Nicholas ^b   Hauswirth, William W ^b  

^a UNIVERSITY OF CALIFORNIA   (United States)

^b UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

^c UNIVERSITY OF CALIFORNIA   (United States)

Author keywords

Gene therapy; Retina; Retinitis pigmentosa

Indexed keywords

GENE PRODUCT;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; GENETIC TRANSDUCTION; HELPER VIRUS; MOUSE; NONHUMAN; PHOTORECEPTOR; PIGMENT EPITHELIUM; PRIORITY JOURNAL; PROMOTER REGION; RAT; RETINA; RETINITIS PIGMENTOSA;

ANIMALS; DEPENDOVIRUS; DNA, RECOMBINANT; GENE EXPRESSION; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; LAC OPERON; MICE; MICE, INBRED C57BL; PHOTORECEPTORS; RATS; RATS, SPRAGUE-DAWLEY; RETINA;

ADENO-ASSOCIATED VIRUS; ADENOVIRIDAE; ANIMALIA; BACTERIA (MICROORGANISMS); MAMMALIA; MURINAE;

EID: 0031011667     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.94.13.6916     Document Type: Article

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