Recombinant adeno-associated viral vectors mediate long-term transgene expression in muscle

Human Gene Therapy

Volumn 8, Issue 6, 1997, Pages 659-669

  Clark, K Reed ^a,b   Sferra, Thomas J ^a,b   Johnson, Philip R ^a,b,c  

^a NATIONWIDE CHILDREN S HOSPITAL   (United States)

^b THE OHIO STATE UNIVERSITY COLLEGE OF MEDICINE   (United States)

^c OHIO STATE UNIVERSITY   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BETA GALACTOSIDASE; BLOOD CLOTTING FACTOR; ERYTHROPOIETIN; INSULIN; SINGLE STRANDED DNA; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ANIMAL EXPERIMENT; ANIMAL TISSUE; ANTIBODY BLOOD LEVEL; ARTICLE; CONTROLLED STUDY; DNA CONFORMATION; ENZYME ACTIVITY; GENE EXPRESSION; GENE TARGETING; GENE THERAPY; GENE TRANSFER; GENETIC TRANSDUCTION; IMMUNE RESPONSE; LYSOSOME STORAGE DISEASE; MALE; MOUSE; MUSCLE CELL; MYOPATHY; NONHUMAN; PROTEIN DEFICIENCY; SKELETAL MUSCLE; TRANSGENE; VIRUS RECOMBINANT;

EID: 0030970938     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.1997.8.6-659     Document Type: Article

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