-
8
-
-
0031691257
-
Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue
-
Erratum, 73:861, 1999.
-
(1998)
J. Virol.
, vol.72
, pp. 8568-8577
-
-
Duan, D.1
Sharma, P.2
Yang, J.3
Yue, Y.4
Dudus, L.5
Zhang, Y.6
Fisher, K.J.7
Engelhardt, J.F.8
-
10
-
-
0027484584
-
Stable in vivo expression of the cystic fibrosis transmembrane conductance regulator with an adeno-associated virus vector
-
(1993)
Proc. Natl. Acad. Sci. USA
, vol.90
, pp. 10613-10617
-
-
Flotte, T.R.1
Afione, S.A.2
Conrad, C.3
McGrath, S.A.4
Solow, R.5
Oka, H.6
Zeitlin, P.L.7
Guggino, W.B.8
Carter, B.J.9
-
11
-
-
0032907636
-
Stable restoration of the sarcoglycan complex in dystrophic muscle perfused with histamine and a recombinant adeno-associated viral vector
-
(1999)
Nat. Med.
, vol.5
, pp. 439-443
-
-
Greelish, J.P.1
Su, L.T.2
Lankford, E.B.3
Burkman, J.M.4
Chen, H.5
Konig, S.K.6
Mercier, I.M.7
Desjardins, P.R.8
Mitchell, M.A.9
Zheng, X.G.10
Leferovich, J.11
Gao, G.P.12
Balice-Gordon, R.J.13
Wilson, J.M.14
Stedman, H.H.15
-
13
-
-
17444387438
-
Long-term correction of canine henophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector
-
(1999)
Nat. Med.
, vol.5
, pp. 56-63
-
-
Herzog, R.W.1
Yang, E.Y.2
Couto, L.B.3
Hagstrom, J.N.4
Elwell, D.5
Fields, P.A.6
Burton, M.7
Bellinger, D.A.8
Read, M.S.9
Brinkhous, K.M.10
Podsakoff, G.M.11
Nichols, T.C.12
Kurtzman, G.J.13
High, K.A.14
-
18
-
-
0034050904
-
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
-
(2000)
Nat. Genet.
, vol.24
, pp. 257-261
-
-
Kay, M.A.1
Manno, C.S.2
Ragni, M.V.3
Larson, P.J.4
Couto, L.B.5
McClelland, A.6
Glader, B.7
Chew, A.J.8
Tai, S.J.9
Herzog, R.W.10
Arruda, V.11
Johnson, F.12
Scallan, C.13
Skarsgard, E.14
Flake, A.W.15
High, K.A.16
-
19
-
-
0030451214
-
Gene delivery to skeletal muscle results in sustained expression and systemic delivery of a therapeutic protein
-
(1996)
Proc. Natl. Acad. Sci. USA
, vol.93
, pp. 14082-14087
-
-
Kessler, P.D.1
Podsakoff, G.M.2
Chert, X.3
McQuiston, S.A.4
Colosi, P.C.5
Matelis, L.A.6
Kurtzman, G.J.7
Byrne, B.J.8
-
22
-
-
0031875874
-
Adeno-associated virus vectors can be efficiently produced without helper virus
-
(1998)
Gene Ther.
, vol.5
, pp. 938-945
-
-
Matsushita, T.1
Elliger, S.2
Elliger, C.3
Podsakoff, G.4
Villarreal, L.5
Kurtzman, G.J.6
Iwaki, Y.7
Colosi, P.8
-
25
-
-
0034202522
-
Inclusion of the hepatic locus control region, an intron, and untranslated region increases and stabilizes hepatic factor IX gene expression in vivo but not in vitro
-
(2000)
Mol. Ther.
, vol.1
, pp. 522-532
-
-
Miao, C.H.1
Ohashi, K.2
Patijn, G.A.3
Meuse, L.4
Ye, X.5
Thompson, A.R.6
Kay, M.A.7
-
26
-
-
0031838721
-
Adeno-associated viral vector-mediated gene transfer of human blood coagulation factor IX into mouse liver
-
(1998)
Blood
, vol.91
, pp. 4600-4607
-
-
Nakai, H.1
Herzog, R.W.2
Hagstrom, J.N.3
Walter, J.4
Kung, S.H.5
Yang, E.Y.6
Tai, S.J.7
Iwaki, Y.8
Kurtzman, G.J.9
Fisher, K.J.10
Colosi, P.11
Couto, L.B.12
High, K.A.13
-
28
-
-
0033814178
-
Recruitment of single-stranded recombinant adeno-associated virus vector genomes and intermolecular recombination are responsible for stable transduction of liver in vivo
-
(2000)
J. Virol.
, vol.74
, pp. 945-9463
-
-
Nakai, H.1
Storm, T.A.2
Kay, M.A.3
-
29
-
-
0030765997
-
Persistence of recombinant adenovirus in vivo is not dependent on vector DNA replication
-
(1997)
J. Virol.
, vol.71
, pp. 8902-8907
-
-
Nelson, J.E.1
Kay, M.A.2
-
30
-
-
0028222954
-
Efficient and sustained gene expression in primary T lymphocytes and primary and cultured tumor cells mediated by adeno-associated virus plasmid DNA complexed to cationic liposomes
-
(1994)
Mol. Cell Biol.
, vol.14
, pp. 2411-2418
-
-
Philip, R.1
Brunette, E.2
Kilinski, L.3
Murugesh, D.4
McNally, M.A.5
Ucar, K.6
Rosenblatt, J.7
Okarma, T.B.8
Lebkowski, J.S.9
-
34
-
-
0030997346
-
Persistent and therapeutic concentrations of human factor IX in mice after hepatic gene transfer of recombinant AAV vectors
-
(1997)
Nat Genet.
, vol.16
, pp. 270-276
-
-
Snyder, R.O.1
Miao, C.H.2
Patijn, G.A.3
Spratt, S.K.4
Danos, O.5
Nagy, D.6
Gown, A.M.7
Winther, B.8
Meuse, L.9
Cohen, L.K.10
Thompson, A.R.11
Kay, M.A.12
-
35
-
-
0030671462
-
Efficient and stable adeno-associated virus-mediated transduction in the skeletal muscle of adult immunocompetent mice
-
(1997)
Hum. Gene Ther.
, vol.8
, pp. 1891-1900
-
-
Snyder, R.O.1
Spratt, S.K.2
Lagarde, C.3
Bohl, D.4
Kaspar, B.5
Sloan, B.6
Cohen, L.K.7
Danos, O.8
-
36
-
-
17444372024
-
Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors
-
(1999)
Nat. Med.
, vol.5
, pp. 64-70
-
-
Snyder, R.O.1
Miao, C.2
Meuse, L.3
Tubb, J.4
Donahue, B.A.5
Lin, H.F.6
Stafford, D.W.7
Patel, S.8
Thompson, A.R.9
Nichols, T.10
Read, M.S.11
Bellinger, D.A.12
Brinkhous, K.M.13
Kay, M.A.14
-
39
-
-
0033022349
-
Safety and biological efficacy of an adeno-associated virus vector-cystic fibrosis transmembrane regulator (AAV-CFFR) in the cystic fibrosis maxillary sinus
-
(1999)
Laryngoscope
, vol.109
, pp. 266-274
-
-
Wagner, J.A.1
Messner, A.H.2
Moran, M.L.3
Daifuku, R.4
Kouyama, K.5
Desch, J.K.6
Manley, S.7
Norbash, A.M.8
Conrad, C.K.9
Friborg, S.10
Reynolds, T.11
Guggino, W.B.12
Moss, R.B.13
Carter, B.J.14
Wine, J.J.15
Flotte, T.R.16
Gardner, P.17
-
45
-
-
0030827586
-
Cellular recombination pathways and viral terminal repeat hairpin structures are sufficient for adeno-associated virus integration in vivo and in vitro
-
(1997)
J. Virol.
, vol.71
, pp. 9231-9247
-
-
Yang, C.C.1
Xiao, X.2
Zhu, X.3
Ansardi, D.C.4
Epstein, N.D.5
Frey, M.R.6
Matera, A.G.7
Samulski, R.J.8
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