Hematopoietic Gene Therapies for Metabolic and Neurologic Diseases

Hematology/Oncology Clinics of North America

Volumn 31, Issue 5, 2017, Pages 869-881

  Biffi, Alessandra ^a  

^a HARVARD MEDICAL SCHOOL   (United States)

Author keywords

Degeneration; Gene therapy; Hematopoietic stem cells; Nervous system; Storage

Indexed keywords

CARBON TETRACHLORIDE; INTERLEUKIN 1ALPHA; INTERLEUKIN 8; LENTIVIRUS VECTOR; MONOCYTE CHEMOTACTIC PROTEIN 1;

ADRENOLEUKODYSTROPHY; ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION; BONE MARROW CELL; CELL BASED GENE THERAPY; CELL DIFFERENTIATION; CELL EXPANSION; CELL MATURATION; CELL ORGANELLE; CELL POPULATION; CELL PROLIFERATION; GENETIC ENGINEERING; GLIOSIS; HEMATOPOIETIC CELL; HEMATOPOIETIC STEM CELL; HOMEOSTASIS; HUMAN; KUPFFER CELL; MACROPHAGE; METABOLIC DISORDER; MICROGLIA; MORPHOLOGY; NEUROFIBRILLARY TANGLE; NEUROLOGIC DISEASE; NEUROPROTECTION; NONHUMAN; OSTEOCLAST; PLASTICITY; PRIORITY JOURNAL; PROGENY; PROTEIN BINDING; REVIEW; SIGNAL TRANSDUCTION; VIRAL GENE DELIVERY SYSTEM; ADVERSE EFFECTS; ANIMAL; CYTOLOGY; GENE EXPRESSION; GENE THERAPY; GENE VECTOR; GENETIC TRANSDUCTION; GENETICS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; METABOLIC DISEASES; METABOLISM; NERVOUS SYSTEM DISEASES; PROCEDURES; TRANSGENE;

ANIMALS; GENE EXPRESSION; GENETIC ENGINEERING; GENETIC THERAPY; GENETIC VECTORS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMATOPOIETIC STEM CELLS; HUMANS; METABOLIC DISEASES; MICROGLIA; NERVOUS SYSTEM DISEASES; TRANSDUCTION, GENETIC; TRANSGENES;

EID: 85025150621     PISSN: 08898588     EISSN: 15581977     Source Type: Journal    
DOI: 10.1016/j.hoc.2017.06.004     Document Type: Review

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