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Volumn 19, Issue 4, 2013, Pages 616-624

Neurodevelopmental Outcomes of Umbilical Cord Blood Transplantation in Metachromatic Leukodystrophy

Author keywords

Metachromatic leukodystrophy; Neurodevelopmental function; Transplantation outcomes

Indexed keywords

ADOLESCENT; ARTICLE; CHEMOTHERAPY; CHILD; CLINICAL ARTICLE; CLINICAL EVALUATION; COGNITIVE DEVELOPMENT; CONTROLLED STUDY; CORD BLOOD STEM CELL TRANSPLANTATION; CORRELATION ANALYSIS; DISEASE COURSE; ENGRAFTMENT; EVOKED RESPONSE; FEMALE; GRAFT VERSUS HOST REACTION; HUMAN; INFANT; INFECTION COMPLICATION; LONGITUDINAL STUDY; MALE; METACHROMATIC LEUKODYSTROPHY; MORTALITY; MOTOR PERFORMANCE; NERVE CELL DIFFERENTIATION; NUCLEAR MAGNETIC RESONANCE IMAGING; PRESCHOOL CHILD; SCHOOL CHILD; SURVIVAL; TOXICITY; TREATMENT OUTCOME;

EID: 84875507383     PISSN: 10838791     EISSN: 15236536     Source Type: Journal    
DOI: 10.1016/j.bbmt.2013.01.010     Document Type: Article
Times cited : (97)

References (27)
  • 2
    • 0031951918 scopus 로고    scopus 로고
    • Long-term stabilization after bone marrow transplantation in juvenile metachromatic leukodystrophy
    • Kidd D., Nelson J., Jones F., et al. Long-term stabilization after bone marrow transplantation in juvenile metachromatic leukodystrophy. Arch Neurol 1998, 55:98-99.
    • (1998) Arch Neurol , vol.55 , pp. 98-99
    • Kidd, D.1    Nelson, J.2    Jones, F.3
  • 3
    • 0029013748 scopus 로고
    • Juvenile metachromatic leukodystrophy: neurological outcome two years after bone marrow transplantation
    • Guffon N., Souillet G., Maire I., et al. Juvenile metachromatic leukodystrophy: neurological outcome two years after bone marrow transplantation. J Inherit Metab Dis 1995, 18:159-161.
    • (1995) J Inherit Metab Dis , vol.18 , pp. 159-161
    • Guffon, N.1    Souillet, G.2    Maire, I.3
  • 4
    • 0029933843 scopus 로고    scopus 로고
    • Late juvenile metachromatic leukodystrophy treated with bone marrow transplantation: a 4-year follow-up study
    • Navarro C., Fernandez J.M., Dominguez C., et al. Late juvenile metachromatic leukodystrophy treated with bone marrow transplantation: a 4-year follow-up study. Neurology 1996, 46:254-256.
    • (1996) Neurology , vol.46 , pp. 254-256
    • Navarro, C.1    Fernandez, J.M.2    Dominguez, C.3
  • 5
    • 0025022733 scopus 로고
    • Treatment of late infantile metachromatic leukodystrophy by bone marrow transplantation
    • Krivit W., Shapiro E., Kennedy W., et al. Treatment of late infantile metachromatic leukodystrophy by bone marrow transplantation. N Engl J Med 1990, 322:54-55.
    • (1990) N Engl J Med , vol.322 , pp. 54-55
    • Krivit, W.1    Shapiro, E.2    Kennedy, W.3
  • 6
    • 0026670348 scopus 로고
    • White matter dysfunction and its neurophysiological correlates: longitudinal study of a case of metachromatic leukodystrophy treated with bone marrow transplantation
    • Shapiro E.G., Lipton M.E., Krivit W. White matter dysfunction and its neurophysiological correlates: longitudinal study of a case of metachromatic leukodystrophy treated with bone marrow transplantation. J Clin Exp Neuropsychol 1992, 14:610-624.
    • (1992) J Clin Exp Neuropsychol , vol.14 , pp. 610-624
    • Shapiro, E.G.1    Lipton, M.E.2    Krivit, W.3
  • 7
    • 0030036466 scopus 로고    scopus 로고
    • Clinical outcome in four children with metachromatic leukodystrophy treated by bone marrow transplantation
    • Malm G., Ringden O., Winiarski J., et al. Clinical outcome in four children with metachromatic leukodystrophy treated by bone marrow transplantation. Bone Marrow Transplant 1996, 17:1003-1008.
    • (1996) Bone Marrow Transplant , vol.17 , pp. 1003-1008
    • Malm, G.1    Ringden, O.2    Winiarski, J.3
  • 8
    • 0032910380 scopus 로고    scopus 로고
    • Slow progression of juvenile metachromatic leukodystrophy 6 years after bone marrow transplantation
    • Kapaun P., Dittman R.W., Granitzny B., et al. Slow progression of juvenile metachromatic leukodystrophy 6 years after bone marrow transplantation. J Child Neurol 1999, 14:222-228.
    • (1999) J Child Neurol , vol.14 , pp. 222-228
    • Kapaun, P.1    Dittman, R.W.2    Granitzny, B.3
  • 9
    • 0025891347 scopus 로고
    • Bone marrow transplantation for metabolic diseases with severe neurological symptoms
    • Hoogerbrugge P.M., Brouwer O.F., Fischer A. Bone marrow transplantation for metabolic diseases with severe neurological symptoms. Bone Marrow Transplant 1991, 7(Suppl. 2):71.
    • (1991) Bone Marrow Transplant , vol.7 , Issue.SUPPL. 2 , pp. 71
    • Hoogerbrugge, P.M.1    Brouwer, O.F.2    Fischer, A.3
  • 10
    • 0028005407 scopus 로고
    • Presymptomatic late-infantile metachromatic leukodystrophy treated with bone marrow transplantation
    • Pridjian G., Humbert J., Willis J., et al. Presymptomatic late-infantile metachromatic leukodystrophy treated with bone marrow transplantation. J Pediatr 1994, 125:755-758.
    • (1994) J Pediatr , vol.125 , pp. 755-758
    • Pridjian, G.1    Humbert, J.2    Willis, J.3
  • 11
    • 0002857752 scopus 로고    scopus 로고
    • Hematopoietic stem cell transplantation for metachromatic leukodystrophy prior to onset of clinical signs and symptoms
    • Westminster Printing Press, London, O. Ringden, J.R. Hobbs, C.G. Steward (Eds.)
    • Peters C., Waye J.S., Vellodi A., et al. Hematopoietic stem cell transplantation for metachromatic leukodystrophy prior to onset of clinical signs and symptoms. Correction of genetic diseases by transplantation, edition IV (COGENT IV) 1997, 34-48. Westminster Printing Press, London. O. Ringden, J.R. Hobbs, C.G. Steward (Eds.).
    • (1997) Correction of genetic diseases by transplantation, edition IV (COGENT IV) , pp. 34-48
    • Peters, C.1    Waye, J.S.2    Vellodi, A.3
  • 12
    • 33847256390 scopus 로고    scopus 로고
    • Early marrow transplantation in a pre-symptomatic neonate with late infantile metachromatic leukodystrophy does not halt disease progression
    • Bredius R.G., Laan L.A., Lankester A.C., et al. Early marrow transplantation in a pre-symptomatic neonate with late infantile metachromatic leukodystrophy does not halt disease progression. Bone Marrow Transplant 2007, 39:309-310.
    • (2007) Bone Marrow Transplant , vol.39 , pp. 309-310
    • Bredius, R.G.1    Laan, L.A.2    Lankester, A.C.3
  • 13
    • 20844453744 scopus 로고    scopus 로고
    • Transplantation of umbilical-cord blood in babies with infantile Krabbe's disease
    • Escolar M.L., Poe M.D., Provenzale J.M., et al. Transplantation of umbilical-cord blood in babies with infantile Krabbe's disease. N Engl J Med 2005, 352:2069-2081.
    • (2005) N Engl J Med , vol.352 , pp. 2069-2081
    • Escolar, M.L.1    Poe, M.D.2    Provenzale, J.M.3
  • 14
    • 2342535103 scopus 로고    scopus 로고
    • Cord-blood transplants from unrelated donors in patients with Hurler's syndrome
    • Staba S.L., Escolar M.L., Poe M., et al. Cord-blood transplants from unrelated donors in patients with Hurler's syndrome. N Engl J Med 2004, 350:1960-1969.
    • (2004) N Engl J Med , vol.350 , pp. 1960-1969
    • Staba, S.L.1    Escolar, M.L.2    Poe, M.3
  • 15
    • 34248668484 scopus 로고    scopus 로고
    • Outcomes of unrelated umbilical cord blood transplantation for X-linked adrenoleukodystrophy
    • Beam D., Poe M.D., Provenzale J.M., et al. Outcomes of unrelated umbilical cord blood transplantation for X-linked adrenoleukodystrophy. Biol Blood Marrow Transplant 2007, 13:665-674.
    • (2007) Biol Blood Marrow Transplant , vol.13 , pp. 665-674
    • Beam, D.1    Poe, M.D.2    Provenzale, J.M.3
  • 16
    • 53449089638 scopus 로고    scopus 로고
    • Unrelated donor umbilical cord blood transplantation for inherited metabolic disorders in 159 pediatric patients from a single center: influence of cellular composition of the graft on transplantation outcomes
    • Prasad V.K., Mendizabal A., Parikh S.H., et al. Unrelated donor umbilical cord blood transplantation for inherited metabolic disorders in 159 pediatric patients from a single center: influence of cellular composition of the graft on transplantation outcomes. Blood 2008, 112:2979-2989.
    • (2008) Blood , vol.112 , pp. 2979-2989
    • Prasad, V.K.1    Mendizabal, A.2    Parikh, S.H.3
  • 17
    • 75149118776 scopus 로고    scopus 로고
    • Cord blood banking for clinical transplantation
    • Rubinstein P. Cord blood banking for clinical transplantation. Bone Marrow Transplant 2009, 10:635-642.
    • (2009) Bone Marrow Transplant , vol.10 , pp. 635-642
    • Rubinstein, P.1
  • 18
    • 31344470473 scopus 로고    scopus 로고
    • Results of the cord blood transplantation study (COBLT): outcomes of unrelated umbilical cord transplantation in pediatric patients with lysosomal and peroxisomal storage disorders
    • Martin P.L., Carter S.L., Kernan N.A., et al. Results of the cord blood transplantation study (COBLT): outcomes of unrelated umbilical cord transplantation in pediatric patients with lysosomal and peroxisomal storage disorders. Biol Blood Marrow Transplant 2006, 12:184-194.
    • (2006) Biol Blood Marrow Transplant , vol.12 , pp. 184-194
    • Martin, P.L.1    Carter, S.L.2    Kernan, N.A.3
  • 25
    • 41049098690 scopus 로고    scopus 로고
    • Methods for assessing neurodevelopment in lysosomal storage diseases and related disorders: a multidisciplinary perspective
    • Martin H.R., Poe M.D., Reinhartsen D., et al. Methods for assessing neurodevelopment in lysosomal storage diseases and related disorders: a multidisciplinary perspective. Acta Paediatr 2008, 97(Suppl.):69-75.
    • (2008) Acta Paediatr , vol.97 , Issue.SUPPL. , pp. 69-75
    • Martin, H.R.1    Poe, M.D.2    Reinhartsen, D.3
  • 26
    • 0033364267 scopus 로고    scopus 로고
    • Globoid cell leukodystrophy: distinguishing early-onset from late-onset disease using a brain MR imaging scoring method
    • Loes D.J., Peters C., Krivit W. Globoid cell leukodystrophy: distinguishing early-onset from late-onset disease using a brain MR imaging scoring method. AJNR Am J Neuroradiol 1999, 20:316-323.
    • (1999) AJNR Am J Neuroradiol , vol.20 , pp. 316-323
    • Loes, D.J.1    Peters, C.2    Krivit, W.3
  • 27
    • 0033616908 scopus 로고    scopus 로고
    • Estimation of failure probabilities in the presence of competing risks: New representations of old estimators
    • Gooley T.A., Leisenring W., Crowley J., Storer B.E. Estimation of failure probabilities in the presence of competing risks: New representations of old estimators. Stat Med 1999, 18:695-706.
    • (1999) Stat Med , vol.18 , pp. 695-706
    • Gooley, T.A.1    Leisenring, W.2    Crowley, J.3    Storer, B.E.4


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.