Genome editing technologies: Defining a path to clinic

Molecular Therapy

Volumn 23, Issue 5, 2015, Pages 796-806

  Corrigan Curay, Jacqueline ^a   O'Reilly, Marina ^a   Kohn, Donald B ^b   Cannon, Paula M ^c   Bao, Gang ^d   Bushman, Frederic D ^e   Carroll, Dana ^f   Cathomen, Toni ^g   Joung, J Keith ^h,i   Roth, David ^e   Sadelain, Michel ^j   Scharenberg, Andrew M ^k   Von Kalle, Christof ^l   Zhang, Feng ^m   Jambou, Robert ^a   Rosenthal, Eugene ^a   Hassani, Morad ^a   Singh, Aparna ^a   Porteus, Matthew H ⁿ  

^a NATIONAL INSTITUTES OF HEALTH   (United States)

^b UNIVERSITY OF CALIFORNIA   (United States)

^c UNIVERSITY OF SOUTHERN CALIFORNIA   (United States)

^d GEORGIA INSTITUTE OF TECHNOLOGY   (United States)

^e UNIVERSITY OF PENNSYLVANIA   (United States)

^f UNIVERSITY OF UTAH SCHOOL OF MEDICINE   (United States)

^g UNIVERSITY OF FREIBURG   (Germany)

^h MASSACHUSETTS GENERAL HOSPITAL   (United States)

ⁱ HARVARD MEDICAL SCHOOL   (United States)

^j MEMORIAL SLOAN KETTERING CANCER CENTER   (United States)

^k UNIVERSITY OF WASHINGTON SCHOOL OF MEDICINE   (United States)

^l GERMAN CANCER RESEARCH CENTER DKFZ   (Germany)

^m HARVARD UNIVERSITY   (United States)

ⁿ STANFORD UNIVERSITY   (United States)

more..

Author keywords

[No Author keywords available]

Indexed keywords

ANTIVIRUS AGENT; CAS9 PROTEIN; CELL PROTEIN; GENOMIC DNA; MEGANUCLEASE; NUCLEASE; SB 728T; TRANSCRIPTION ACTIVATOR LIKE EFFECTOR NUCLEASE; UNCLASSIFIED DRUG; ZINC FINGER NUCLEASE;

CHROMOSOME REARRANGEMENT; CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEAT; CONFERENCE PAPER; CYTOTOXICITY ASSAY; DNA MODIFICATION; DNA SEQUENCE; DOUBLE STRANDED DNA BREAK; GENE FUNCTION; GENE IDENTIFICATION; GENE TECHNOLOGY; GENOME ANALYSIS; GENOME EDITING TECHNOLOGY; GENOTOXICITY ASSAY; HUMAN; HUMAN IMMUNODEFICIENCY VIRUS; MEDICAL RESEARCH; MOLECULAR DYNAMICS; NONHUMAN; PROCESS DESIGN; SEQUENCE ANALYSIS; SIGNAL TRANSDUCTION; VIRUS LOAD; ANIMAL; ANIMAL MODEL; DNA REPAIR; GENE REARRANGEMENT; GENETIC ENGINEERING; GENOME; GENOMICS; MUTAGEN TESTING; PROCEDURES; TRANSLATIONAL RESEARCH;

ANIMALS; DNA BREAKS, DOUBLE-STRANDED; DNA REPAIR; GENE REARRANGEMENT; GENETIC ENGINEERING; GENOME; GENOMICS; HUMANS; MODELS, ANIMAL; MUTAGENICITY TESTS; TRANSLATIONAL MEDICAL RESEARCH;

EID: 84928948209     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2015.54     Document Type: Conference Paper

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