Fetal gene therapy: Recent advances and current challenges

Expert Opinion on Biological Therapy

Volumn 11, Issue 10, 2011, Pages 1257-1271

  Mattar, Citra N ^a   Choolani, Mahesh ^a   Biswas, Arijit ^a   Waddington, Simon N ^b   Chan, Jerry K Y ^a,c,d  

^a NATIONAL UNIVERSITY OF SINGAPORE   (Singapore)

^b UNIVERSITY COLLEGE LONDON   (United Kingdom)

^c KK WOMEN'S AND CHILDREN'S HOSPITAL   (Singapore)

^d DUKE NUS MEDICAL SCHOOL   (Singapore)

Author keywords

Adverse events; Animal models; Clinical translation; Efficacy; Ethics; Fetal gene therapy; Safety

Indexed keywords

ADENOVIRUS VECTOR; INTERLEUKIN 10; RETROVIRUS VECTOR;

CARCINOGENESIS; EX VIVO GENE TRANSFER; FETUS GENE THERAPY; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; GERM LINE GENE THERAPY; GESTATIONAL AGE; HUMAN; IN VIVO GENE TRANSFER; MONOGENIC DISORDER; MUTAGENESIS; NONHUMAN; REVIEW; RHEUMATOID ARTHRITIS;

ANIMALS; DISEASE MODELS, ANIMAL; FEMALE; FETAL DISEASES; FETAL THERAPIES; GENE THERAPY; GENETIC VECTORS; GERM CELLS; HUMANS; PREGNANCY;

ANIMALIA; PRIMATES;

EID: 80052499615     PISSN: 14712598     EISSN: None     Source Type: Journal    
DOI: 10.1517/14712598.2011.585153     Document Type: Review

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