Full-length dystrophin gene transfer to the mdx mouse in utero

Gene Therapy

Volumn 15, Issue 7, 2008, Pages 531-536

  Reay, D P ^a   Bilbao, R ^a   Koppanati, B M ^a   Cai, L ^a   O'Day, T L ^b   Jiang, Z ^a   Zheng, H ^a   Watchko, J F ^b   Clemens, P R ^a,c  

^a UNIVERSITY OF PITTSBURGH SCHOOL OF MEDICINE   (United States)

^b UNIVERSITY OF PITTSBURGH   (United States)

^c VETERANS AFFAIRS MEDICAL CENTER   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; DYSTROPHIN; RECOMBINANT PROTEIN;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL DEGENERATION; CELL NUCLEUS; CELL PROTECTION; CELL REGENERATION; CONTROLLED STUDY; DUCHENNE MUSCULAR DYSTROPHY; FEMALE; FETAL THERAPY; FETUS; GENE TARGETING; GENE TRANSFER; HINDLIMB; MOUSE; MUSCLE CELL; MUSCLE FORCE; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION; TIBIALIS ANTERIOR MUSCLE; X CHROMOSOME LINKED MUSCULAR DYSTROPHIC MOUSE;

ADENOVIRIDAE; ANIMALS; ANIMALS, NEWBORN; DYSTROPHIN; FEMALE; FETAL THERAPIES; GENE EXPRESSION; GENE THERAPY; GENETIC VECTORS; HINDLIMB; INJECTIONS, INTRAMUSCULAR; MICE; MICE, INBRED MDX; MUSCLE, SKELETAL; MUSCULAR DYSTROPHY, ANIMAL; MUSCULAR DYSTROPHY, DUCHENNE; RECOMBINANT PROTEINS; TRANSDUCTION, GENETIC;

ANIMALIA; MURINAE;

EID: 40949120900     PISSN: 09697128     EISSN: 14765462     Source Type: Journal    
DOI: 10.1038/gt.2008.8     Document Type: Article

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