Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

Nature Medicine

Volumn 5, Issue 1, 1999, Pages 56-63

  Herzog, Roland W ^a   Yang, Edmund Y ^b   Couto, Linda B ^c   Hagstrom, J Nathan ^a   Elwell, Dan ^d   Fields, Paul A ^a   Burton, Melissa ^c   Bellinger, Dwight A ^d   Read, Marjorie S ^d   Brinkhous, Kenneth M ^d   Podsakoff, Gregory M ^c   Nichols, Timothy C ^d   Kurtzman, Gary J ^c   High, Katherine A ^a,e  

^a HOSPITAL OF THE UNIVERSITY OF PENNSYLVANIA   (United States)

^b CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

^c Avigen Inc   (United States)

^d UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

^e UNIVERSITY OF PENNSYLVANIA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BLOOD CLOTTING FACTOR 9; VIRUS VECTOR;

ADENOVIRUS; ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; BLOOD CLOTTING; BLOOD CLOTTING TIME; DNA DETERMINATION; DOG; GENE EXPRESSION REGULATION; GENE TARGETING; GENE THERAPY; HEMOPHILIA B; IMMUNOFLUORESCENCE TEST; MALE; NONHUMAN; PRIORITY JOURNAL; PROTEIN EXPRESSION;

ANIMALS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; DNA, VIRAL; DOGS; FACTOR IX; GENE EXPRESSION; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HEMOPHILIA B; HUMANS; INJECTIONS, INTRAMUSCULAR; MALE; TIME FACTORS; TUMOR CELLS, CULTURED;

ADENOVIRIDAE; ANIMALIA; CANIS FAMILIARIS;

EID: 17444387438     PISSN: 10788956     EISSN: None     Source Type: Journal    
DOI: 10.1038/4743     Document Type: Article

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