Genetically corrected autologous stem cells engraft, but host immune responses limit their utility in canine α-L-iduronidase deficiency

Blood

Volumn 93, Issue 6, 1999, Pages 1895-1905

  Lutzko, Carolyn ^b   Kruth, Stephen ^b   Abrams Ogg, Anthony C G ^b   Lau, Kathy ^b   Li, Liheng ^b   Clark, Brian R ^b   Ruedy, Christine ^b   Nanji, Shaherose ^b   Foster, Robert ^b   Kohn, Donald ^b   Shull, Robert ^b   Dubé, Ian D ^a  

^a SUNNYBROOK RESEARCH INSTITUTE   (Canada)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

CYCLOSPORIN A; VIRUS VECTOR;

ADOPTIVE TRANSFER; ANIMAL MODEL; ARTICLE; CLINICAL ARTICLE; CLINICAL FEATURE; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER; HEMATOPOIETIC STEM CELL; HURLER SYNDROME; IMMUNE RESPONSE; NONHUMAN; PATHOPHYSIOLOGY; PRIORITY JOURNAL;

ANIMALS; BONE MARROW CELLS; CELLS, CULTURED; CULTURE MEDIA; DOGS; GENE EXPRESSION; GENE THERAPY; GENE TRANSFER TECHNIQUES; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMATOPOIETIC STEM CELLS; HUMANS; IDURONIDASE; IMMUNITY; IMMUNITY, CELLULAR; LYMPHOCYTE ACTIVATION; MUCOPOLYSACCHARIDOSIS I; POLYMERASE CHAIN REACTION; RETROVIRIDAE; TRANSPLANTATION, AUTOLOGOUS;

EID: 0033559722     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Article

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