Insights gained from gene therapy in animal models of retGC1 deficiency

Frontiers in Molecular Neuroscience

Volumn 7, Issue MAY, 2014, Pages

  Boye, Shannon E ^a  

^a UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

Author keywords

AAV; GC1; Guanylate cyclase; GUCY2D; LCA1; Leber congenital amaurosis; retGC1; Retinal gene therapy

Indexed keywords

GUANYLATE CYCLASE; RETINAL GUANYLATE CYCLASE; UNCLASSIFIED DRUG;

BEHAVIOR; COLOR VISION; ELECTRORETINOGRAPHY; GENE EXPRESSION; GENE MUTATION; GENE REPLACEMENT THERAPY; GENE THERAPY; HUMAN; LEBER CONGENITAL AMAUROSIS; NONHUMAN; PHOTORECEPTOR; PHOTOTRANSDUCTION; RETINA DEGENERATION; REVIEW;

EID: 84901328985     PISSN: 16625099     EISSN: None     Source Type: Journal    
DOI: 10.3389/fnmol.2014.00043     Document Type: Review

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