Restoration of vision in the PDE6β-deficient dog, a large animal model of rod-cone dystrophy

Molecular Therapy

Volumn 20, Issue 11, 2012, Pages 2019-2030

  Petit, Lolita ^a   Lhériteau, Elsa ^a   Weber, Michel ^b   Le Meur, Guylène ^b   Deschamps, Jack Yves ^c   Provost, Nathalie ^a   Mendes Madeira, Alexandra ^a   Libeau, Lyse ^a   Guihal, Caroline ^a   Colle, Marie Anne ^d   Moullier, Philippe ^a,c,e   Rolling, Fabienne ^a  

^a UNIVERSITÉ DE NANTES   (France)

^b HÔTEL DIEU   (France)

^c LUNAM UNIVERSITÉ   (France)

^d HÔTEL DIEU   (France)

^e UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

PARVOVIRUS VECTOR; PHOSPHODIESTERASE VI; PHOSPHODIESTERASE VI BETA SUBUNIT; RHODOPSIN KINASE; UNCLASSIFIED DRUG;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; AUTOPSY; CONTROLLED STUDY; DOG; ELECTRORETINOGRAPHY; GENE EXPRESSION; IN VIVO STUDY; NONHUMAN; PROMOTER REGION; RETINA CONE; RETINA DEGENERATION; RETINITIS PIGMENTOSA; ROD CONE DYSPLASIA TYPE 1; ROD CONE DYSTROPHY; TRANSGENE; VIRAL GENE THERAPY; VIRUS RECOMBINANT; VISION;

ADENO-ASSOCIATED VIRUS; ANIMALIA; CANIS FAMILIARIS;

EID: 84869089744     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2012.134     Document Type: Article

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