AAV-mediated gene therapy in mouse models of recessive retinal degeneration

Current Molecular Medicine

Volumn 12, Issue 3, 2012, Pages 316-330

  Pang, J J ^a,b   Lei, L ^c   Dai, X ^a   Shi, W ^b   Liu, X ^b   Dinculescu, A ^b   McDowell, J H ^b  

^a WENZHOU MEDICAL UNIVERSITY   (China)

^b UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

^c SUN YAT SEN UNIVERSITY   (China)

Author keywords

Adeno associated viral vector; Gene therapy; Inherited retinal disease; Monogenic recessive mutation; Mouse model

Indexed keywords

ARYL HYDROCARBON INTERACTING PROTEIN LIKE 1; LECITHIN RETINOL ACYL TRANSFERASE; MEMBRANE PROTEIN; UNCLASSIFIED DRUG;

ADENO ASSOCIATED VIRUS; BEHAVIOR; COLOR BLINDNESS; ELECTRORETINOGRAPHY; GENE MUTATION; GENE THERAPY; GENETIC RECOMBINATION; HUMAN; LEBER CONGENITAL AMAUROSIS; MORPHOLOGY; MOUSE; MUTANT; NONHUMAN; RECESSIVE INHERITANCE; RECESSIVE RETINAL DEGENERATION; RETINA DEGENERATION; RETINITIS PIGMENTOSA; RETINOSCHISIS; REVIEW; SEROTYPE; STARGARDT DISEASE; USHER SYNDROME; VISION; WILD TYPE; X LINKED JUVENILE RETINOSCHISIS;

ANIMALS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; GENE THERAPY; GENETIC VECTORS; MICE; RETINAL DEGENERATION;

ANIMALIA;

EID: 84863115790     PISSN: 15665240     EISSN: 18755666     Source Type: Journal    
DOI: 10.2174/156652412799218877     Document Type: Review

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