Rescue of photoreceptor function by AAV-mediated gene transfer in a mouse model of inherited retinal degeneration

Gene Therapy

Volumn 4, Issue 7, 1997, Pages 683-690

  Jomary, C ^a   Vincent, K A ^b   Grist, J ^a   Neal, M J ^a   Jones, S E ^a  

^a ST THOMAS HOSPITAL   (United Kingdom)

^b GENZYME CORPORATION   (United States)

Author keywords

Adeno associated virus; Photoreceptor; Retinal degeneration

Indexed keywords

COMPLEMENTARY DNA; OPSIN; PHOSPHODIESTERASE; VIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ANIMAL CELL; ARTICLE; CONTROLLED STUDY; ELECTRORETINOGRAPHY; GENE EXPRESSION; GENE MUTATION; GENE THERAPY; GENE TRANSFER; IMMUNOREACTIVITY; MOUSE; NONHUMAN; PHOTORECEPTOR; PHOTORECEPTOR CELL; PRIORITY JOURNAL; PROMOTER REGION; RECESSIVE GENE; RETINA DEGENERATION; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; TRANSGENE; VIRUS RECOMBINANT;

ADENO-ASSOCIATED VIRUS; ANIMALIA; MURINAE;

EID: 0030759730     PISSN: 09697128     EISSN: None     Source Type: Journal    
DOI: 10.1038/sj.gt.3300440     Document Type: Article

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