Gene insertion into genomic safe harbors for human gene therapy

Molecular Therapy

Volumn 24, Issue 4, 2016, Pages 678-684

  Papapetrou, Eirini P ^a   Schambach, Axel ^b,c  

^a MOUNT SINAI SCHOOL OF MEDICINE   (United States)

^b HANNOVER MEDICAL SCHOOL   (Germany)

^c BOSTON CHILDREN S HOSPITAL   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BIOLOGY; CATALYSIS; GENE INSERTION; GENE TARGETING; GENE THERAPY; HUMAN; REGENERATIVE MEDICINE; VALIDATION PROCESS; GENE EXPRESSION REGULATION; HUMAN GENOME; PROCEDURES; TRANSGENE;

GENETIC THERAPY; GENOME, HUMAN; HUMANS; MUTAGENESIS, INSERTIONAL; TRANSGENES;

EID: 84960192213     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2016.38     Document Type: Review

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