Ribosomal DNA integrating rAAV-rDNA vectors allow for stable transgene expression

Molecular Therapy

Volumn 20, Issue 10, 2012, Pages 1912-1923

  Lisowski, Leszek ^a   Lau, Ashley ^a,b   Wang, Zhongya ^c   Zhang, Yue ^a   Zhang, Feijie ^a   Grompe, Markus ^c   Kay, Mark A ^a  

^a STANFORD UNIVERSITY   (United States)

^b HARVARD MEDICAL SCHOOL   (United States)

^c OREGON HEALTH AND SCIENCE UNIVERSITY   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BLOOD CLOTTING FACTOR 9; GENOMIC DNA; PARVOVIRUS VECTOR; RECOMBINANT PARVOVIRUS VECTOR; RIBOSOME DNA; UNCLASSIFIED DRUG;

ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; CELL DIVISION; CONTROLLED STUDY; DNA FLANKING REGION; DNA SEQUENCE; DRUG SAFETY; FEMALE; GENE CASSETTE; GENE LOCUS; GENE LOSS; GENE TRANSFER; GENETIC MANIPULATION; GENOME SIZE; HOMOLOGOUS RECOMBINATION; IN VIVO STUDY; LIVER REGENERATION; MOUSE; NONHUMAN; NUCLEOTIDE SEQUENCE; PROTEIN BLOOD LEVEL; STABLE EXPRESSION; TRANSGENE; VIRAL GENE DELIVERY SYSTEM; VIRUS DNA CELL DNA INTERACTION;

ADENO-ASSOCIATED VIRUS;

EID: 84866973619     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2012.164     Document Type: Article

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