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Volumn 2014, Issue 3, 2014, Pages

Targeted genome editing by lentiviral protein transduction of zinc-finger and TAL-effector nucleases

Author keywords

Gag; Lentiviral vector; Protein transduction; Transcription activator like effector nucleases; Zinc finger nucleases

Indexed keywords

DNA; RNA; TRANSCRIPTION FACTOR TAL1; VIRUS PROTEIN; VIRUS VECTOR; ZINC FINGER NUCLEASE;

EID: 84899643400     PISSN: None     EISSN: 2050084X     Source Type: Journal    
DOI: 10.7554/eLife.01911     Document Type: Article
Times cited : (23)

References (57)
  • 1
    • 80053343092 scopus 로고    scopus 로고
    • TAL effectors: Customizable proteins for DNA targeting
    • Bogdanove, A.J. and Voytas, D.F. (2011) TAL effectors: customizable proteins for DNA targeting. Science, 333, 1843-1846.
    • (2011) Science , vol.333 , pp. 1843-1846
    • Bogdanove, A.J.1    Voytas, D.F.2
  • 8
    • 84878528467 scopus 로고    scopus 로고
    • Genomic Editing of the HIV-1 Coreceptor CCR5 in Adult Hematopoietic Stem and Progenitor Cells Using Zinc Finger Nucleases
    • Li, L., Krymskaya, L., Wang, J., Henley, J., Rao, A., Cao, L.F., Tran, C.A., Torres-Coronado, M., Gardner, A., Gonzalez, N. et al. (2013) Genomic Editing of the HIV-1 Coreceptor CCR5 in Adult Hematopoietic Stem and Progenitor Cells Using Zinc Finger Nucleases. Mol. Then, 21, 1259-1269.
    • (2013) Mol. Then , vol.21 , pp. 1259-1269
    • Li, L.1    Krymskaya, L.2    Wang, J.3    Henley, J.4    Rao, A.5    Cao, L.F.6    Tran, C.A.7    Torres-Coronado, M.8    Gardner, A.9    Gonzalez, N.10
  • 9
    • 84863297206 scopus 로고    scopus 로고
    • Optimized TAL effector nucleases (TALENs) for use in treatment of sickle cell disease
    • Sun, N., Liang, J., Abil, Z. and Zhao, H. (2012) Optimized TAL effector nucleases (TALENs) for use in treatment of sickle cell disease. Mol. Biosyst, 8, 1255-1263.
    • (2012) Mol. Biosyst , vol.8 , pp. 1255-1263
    • Sun, N.1    Liang, J.2    Abil, Z.3    Zhao, H.4
  • 14
    • 84871949643 scopus 로고    scopus 로고
    • Zinc-finger nuclease-mediated gene correction using single AAV vector transduction and enhancement by Food and Drug Administration-approved drugs
    • Ellis, B.L., Hirsch, M.L., Porter, S.N., Samulski, R.J. and Porteus, M.H. (2013) Zinc-finger nuclease-mediated gene correction using single AAV vector transduction and enhancement by Food and Drug Administration-approved drugs. Gene Ther., 20, 35-42.
    • (2013) Gene Ther , vol.20 , pp. 35-42
    • Ellis, B.L.1    Hirsch, M.L.2    Porter, S.N.3    Samulski, R.J.4    Porteus, M.H.5
  • 16
    • 61449266636 scopus 로고    scopus 로고
    • Attenuation of zinc finger nuclease toxicity by small-molecule regulation of protein levels
    • Pruett-Miller, S.M., Reading, D.W., Porter, S.N. and Porteus, M.H. (2009) Attenuation of zinc finger nuclease toxicity by small-molecule regulation of protein levels. PLoS Genet, 5, el000376.
    • (2009) PLoS Genet , vol.5
    • Pruett-Miller, S.M.1    Reading, D.W.2    Porter, S.N.3    Porteus, M.H.4
  • 17
    • 84864439768 scopus 로고    scopus 로고
    • Targeted gene knockout by direct delivery of zinc-finger nuclease proteins
    • Gaj, T., Guo, J., Kato, Y., Sirk, S.J. and Barbas, C.F., 3rd. (2012) Targeted gene knockout by direct delivery of zinc-finger nuclease proteins. Nat. Methods, 9, 805-807.
    • (2012) Nat. Methods , vol.9 , pp. 805-807
    • Gaj, T.1    Guo, J.2    Kato, Y.3    Sirk, S.J.4    Barbas III, C.F.5
  • 18
    • 84871393255 scopus 로고    scopus 로고
    • Enhancing endosomal escape of transduced proteins by photochemical internalisation
    • Mellert, K., Lamia, M., Scheffzek, K., Wittig, R. and Kaufmann, D. (2012) Enhancing endosomal escape of transduced proteins by photochemical internalisation. PLoS ONE, 7, e52473.
    • (2012) PLoS ONE , vol.7
    • Mellert, K.1    Lamia, M.2    Scheffzek, K.3    Wittig, R.4    Kaufmann, D.5
  • 20
    • 0025277827 scopus 로고
    • Assembly of gag-beta-galactosidase proteins into retrovirus particles
    • Jones, T.A., Blaug, G., Hansen, M. and Barklis, E. (1990) Assembly of gag-beta-galactosidase proteins into retrovirus particles. /. Virol, 64, 2265-2279.
    • (1990) J. Virol , vol.64 , pp. 2265-2279
    • Jones, T.A.1    Blaug, G.2    Hansen, M.3    Barklis, E.4
  • 21
    • 0025075750 scopus 로고
    • Incorporation of chimeric gag protein into retroviral particles
    • Weldon, R.A., Jr., Erdie, C.R., Oliver, M.G. and Wills, J.W. (1990) Incorporation of chimeric gag protein into retroviral particles. J. Virol, 64, 4169-4179.
    • (1990) J. Virol , vol.64 , pp. 4169-4179
    • Weldon Jr., R.A.1    Erdie, C.R.2    Oliver, M.G.3    Wills, J.W.4
  • 23
    • 47049130164 scopus 로고    scopus 로고
    • Imaging the biogenesis of individual HIV-1 virions in live cells
    • Jouvenet, N., Bieniasz, P.D. and Simon, S.M. (2008) Imaging the biogenesis of individual HIV-1 virions in live cells. Nature, 454, 236-240.
    • (2008) Nature , vol.454 , pp. 236-240
    • Jouvenet, N.1    Bieniasz, P.D.2    Simon, S.M.3
  • 24
    • 0028074881 scopus 로고
    • Tethering human immunodeficiency virus 1 integrase to a DNA site directs integration to nearby sequences
    • Bushman, F.D. (1994) Tethering human immunodeficiency virus 1 integrase to a DNA site directs integration to nearby sequences. Proc. Natl. Acad. Sci. U. S. A, 91, 9233-9237.
    • (1994) Proc. Natl. Acad. Sci. U. S. A , vol.91 , pp. 9233-9237
    • Bushman, F.D.1
  • 25
    • 0029655849 scopus 로고    scopus 로고
    • Directed integration of viral DNA mediated by fusion proteins consisting of human immunodeficiency virus type 1 integrase and Escherichia coli LexA protein./
    • Goulaouic, H. and Chow, S.A. (1996) Directed integration of viral DNA mediated by fusion proteins consisting of human immunodeficiency virus type 1 integrase and Escherichia coli LexA protein./ Virol, 70, 37-46.
    • (1996) Virol , vol.70 , pp. 37-46
    • Goulaouic, H.1    Chow, S.A.2
  • 26
    • 0031060377 scopus 로고    scopus 로고
    • Tethering human immunodeficiency virus type 1 preintegration complexes to target DNA promotes integration at nearby sites
    • Bushman, F.D. and Miller, M.D. (1997) Tethering human immunodeficiency virus type 1 preintegration complexes to target DNA promotes integration at nearby sites. J Virol, 71, 458-464.
    • (1997) J Virol , vol.71 , pp. 458-464
    • Bushman, F.D.1    Miller, M.D.2
  • 27
    • 44849100325 scopus 로고    scopus 로고
    • Vprl4-88-Apobec3G fusion protein is efficiently incorporated into Vif-positive HIV-1 particles and inhibits viral infection
    • Ao, Z., Yu, Z., Wang, L., Zheng, Y. and Yao, X. (2008) Vprl4-88-Apobec3G fusion protein is efficiently incorporated into Vif-positive HIV-1 particles and inhibits viral infection. PLoS ONE, 3, el995.
    • (2008) PLoS ONE , vol.3
    • Ao, Z.1    Yu, Z.2    Wang, L.3    Zheng, Y.4    Yao, X.5
  • 28
    • 0034095092 scopus 로고    scopus 로고
    • Packageable antiviral therapeutics against human immunodeficiency virus type 1: Virion-targeted virus inactivation by incorporation of a single-chain antibody against viral integrase into progeny virions
    • Okui, N., Sakuma, R., Kobayashi, N., Yoshikura, H., Kitamura, T., Chiba, J. and Kitamura, Y. (2000) Packageable antiviral therapeutics against human immunodeficiency virus type 1: virion-targeted virus inactivation by incorporation of a single-chain antibody against viral integrase into progeny virions. Hum. Gene Ther, 11, 537-546.
    • (2000) Hum. Gene Ther , vol.11 , pp. 537-546
    • Okui, N.1    Sakuma, R.2    Kobayashi, N.3    Yoshikura, H.4    Kitamura, T.5    Chiba, J.6    Kitamura, Y.7
  • 31
    • 0029039296 scopus 로고
    • Targeting foreign proteins to human immunodeficiency virus particles via fusion with Vpr and Vpx
    • Wu, X., Liu, H., Xiao, H., Kim, J., Seshaiah, P., Natsoulis, G., Boeke, J.D., Hahn, B.H. and Kappes, J.C. (1995) Targeting foreign proteins to human immunodeficiency virus particles via fusion with Vpr and Vpx. J. Virol, 69, 3389-3398.
    • (1995) J. Virol , vol.69 , pp. 3389-3398
    • Wu, X.1    Liu, H.2    Xiao, H.3    Kim, J.4    Seshaiah, P.5    Natsoulis, G.6    Boeke, J.D.7    Hahn, B.H.8    Kappes, J.C.9
  • 32
    • 77957608958 scopus 로고    scopus 로고
    • Site-specific gene insertion mediated by a Cre-loxP-carrying lentiviral vector
    • Michel, G., Yu, Y., Chang, T. and Yee, J.K. (2010) Site-specific gene insertion mediated by a Cre-loxP-carrying lentiviral vector. Mol. Ther, 18, 1814-1821.
    • (2010) Mol. Ther , vol.18 , pp. 1814-1821
    • Michel, G.1    Yu, Y.2    Chang, T.3    Yee, J.K.4
  • 33
    • 80053195536 scopus 로고    scopus 로고
    • Efficient gene targeting mediated by a lentiviral vector-associated meganuclease
    • Izmiryan, A., Basmaciogullari, S., Henry, A., Paques, F. and Danos, O. (2011) Efficient gene targeting mediated by a lentiviral vector-associated meganuclease. Nucleic Acids Res., 39, 7610-7619.
    • (2011) Nucleic Acids Res , vol.39 , pp. 7610-7619
    • Izmiryan, A.1    Basmaciogullari, S.2    Henry, A.3    Paques, F.4    Danos, O.5
  • 34
    • 43049162225 scopus 로고    scopus 로고
    • Snapshot: HIV-1 proteins
    • Swanson, CM. and Malim, M.H. (2008) Snapshot: HIV-1 proteins. Cell, 133, 742, e741.
    • (2008) Cell , vol.133 , Issue.742
    • Swanson, C.M.1    Malim, M.H.2
  • 36
    • 80052564938 scopus 로고    scopus 로고
    • Protein transduction by pseudotyped lentivirus-like nanoparticles
    • Aoki, T., Miyauchi, K., Urano, E., Ichikawa, R. and Komano, J. (2011) Protein transduction by pseudotyped lentivirus-like nanoparticles. Gene Ther, 18, 936-941.
    • (2011) Gene Ther , vol.18 , pp. 936-941
    • Aoki, T.1    Miyauchi, K.2    Urano, E.3    Ichikawa, R.4    Komano, J.5
  • 38
    • 77951971713 scopus 로고    scopus 로고
    • Production of HIV-1 Integrase Fusion Protein-Carrying Lentiviral Vectors for Gene Therapy and Protein Transduction
    • Schenkwein, D., Turkki, V., Hanna-Riikka, K., Airenne, K. and Ylä-Herttuala, S. (2010) Production of HIV-1 Integrase Fusion Protein-Carrying Lentiviral Vectors for Gene Therapy and Protein Transduction. Hum. Gene Ther, 21, 589-602.
    • (2010) Hum. Gene Ther , vol.21 , pp. 589-602
    • Schenkwein, D.1    Turkki, V.2    Hanna-Riikka, K.3    Airenne, K.4    Ylä-Herttuala, S.5
  • 39
    • 58149378581 scopus 로고    scopus 로고
    • Substitution of the myristoylation signal of human immunodeficiency virus type 1 Pr55Gag with the phospholipase C -delta 1 pleckstrin homology domain results in infectious pseudovirion production
    • Urano, E., Aoki, T., Futahashi, Y., Murakami, T., Morikawa, Y., Yamamoto, N. and Komano, J. (2008) Substitution of the myristoylation signal of human immunodeficiency virus type 1 Pr55Gag with the phospholipase C -delta 1 pleckstrin homology domain results in infectious pseudovirion production. J. Gen. Virol, 89, 3144-3149.
    • (2008) J. Gen. Virol , vol.89 , pp. 3144-3149
    • Urano, E.1    Aoki, T.2    Futahashi, Y.3    Murakami, T.4    Morikawa, Y.5    Yamamoto, N.6    Komano, J.7
  • 41
    • 74949133880 scopus 로고    scopus 로고
    • Targeted chromosomal deletions in human cells using zinc finger nucleases
    • Lee, H.J., Kim, E. and Kim, J.S. (2010) Targeted chromosomal deletions in human cells using zinc finger nucleases. Genome Res., 20, 81-89.
    • (2010) Genome Res , vol.20 , pp. 81-89
    • Lee, H.J.1    Kim, E.2    Kim, J.S.3
  • 42
    • 84879264708 scopus 로고    scopus 로고
    • ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering
    • Gaj, T., Gersbach, C.A. and Barbas, C.F., 3rd. (2013) ZFN, TALEN, and CRISPR/Cas-based methods for genome engineering. Trends BiotechnoL, 31,397-405.
    • (2013) Trends BiotechnoL , vol.31 , pp. 397-405
    • Gaj, T.1    Gersbach, C.A.2    Barbas III, C.F.3
  • 44
    • 0033856584 scopus 로고    scopus 로고
    • Localization of human immunodeficiency virus type 1 Gag and Env at the plasma membrane by confocal imaging
    • Hermida-Matsumoto, L. and Resh, M.D. (2000) Localization of human immunodeficiency virus type 1 Gag and Env at the plasma membrane by confocal imaging. J. Virol, 74, 8670-8679.
    • (2000) J. Virol , vol.74 , pp. 8670-8679
    • Hermida-Matsumoto, L.1    Resh, M.D.2
  • 45
    • 36049013150 scopus 로고    scopus 로고
    • Sequence of human immunodeficiency virus type 1 (HIV-1) Gag localization and oligomerization monitored with live confocal imaging of a replication-competent, fluorescently tagged HIV-1
    • Hubner, W., Chen, P., Del Portillo, A., Liu, Y., Gordon, R.E. and Chen, B.K. (2007) Sequence of human immunodeficiency virus type 1 (HIV-1) Gag localization and oligomerization monitored with live confocal imaging of a replication-competent, fluorescently tagged HIV-1. J Virol, 81, 12596-12607.
    • (2007) J Virol , vol.81 , pp. 12596-12607
    • Hubner, W.1    Chen, P.2    Del Portillo, A.3    Liu, Y.4    Gordon, R.E.5    Chen, B.K.6
  • 46
    • 84883743436 scopus 로고    scopus 로고
    • Integrase-defective lentiviral vectors as a delivery platform for targeted modification of adenosine deaminase locus
    • Joglekar, A.V., Hollis, R.P., Kuftinec, G., Senadheera, S., Chan, R. and Kohn, D.B. (2013) Integrase-defective lentiviral vectors as a delivery platform for targeted modification of adenosine deaminase locus. Mol Ther., 21, 1705-1717.
    • (2013) Mol Ther , vol.21 , pp. 1705-1717
    • Joglekar, A.V.1    Hollis, R.P.2    Kuftinec, G.3    Senadheera, S.4    Chan, R.5    Kohn, D.B.6
  • 47
    • 0034124697 scopus 로고    scopus 로고
    • Genetic reassortment and patch repair by recombination in retroviruses
    • Mikkelsen, J.G. and Pedersen, F.S. (2000) Genetic reassortment and patch repair by recombination in retroviruses. J Biomed. Sci., 7, 77-99.
    • (2000) J Biomed. Sci , vol.7 , pp. 77-99
    • Mikkelsen, J.G.1    Pedersen, F.S.2
  • 48
    • 44949162060 scopus 로고    scopus 로고
    • Targeted gene inactivation in zebrafish using engineered zinc-finger nucleases
    • Meng, X., Noyes, M.B., Zhu, L.J., Lawson, N.D. and Wolfe, S.A. (2008) Targeted gene inactivation in zebrafish using engineered zinc-finger nucleases. Nat. Biotechnol, 26, 695-701.
    • (2008) Nat. Biotechnol , vol.26 , pp. 695-701
    • Meng, X.1    Noyes, M.B.2    Zhu, L.J.3    Lawson, N.D.4    Wolfe, S.A.5
  • 51
    • 0038523969 scopus 로고    scopus 로고
    • Chimeric nucleases stimulate gene targeting in human cells
    • Porteus, M.H. and Baltimore, D. (2003) Chimeric nucleases stimulate gene targeting in human cells. Science, 300, 763.
    • (2003) Science , vol.300 , pp. 763
    • Porteus, M.H.1    Baltimore, D.2
  • 52
    • 84860999625 scopus 로고    scopus 로고
    • Development of transgenic cloned pig models of skin inflammation by DNA transposon-directed ectopic expression of human betal and alpha2 integrin
    • Staunstrup, N.H., Madsen, J., Primo, M.N., Li, J., Liu, Y., Kragh, P.M., Li, R., Schmidt, M., Purup, S., Dagnaes-Hansen, F. et al. (2012) Development of transgenic cloned pig models of skin inflammation by DNA transposon-directed ectopic expression of human betal and alpha2 integrin. PLoS ONE,7,e36658.
    • (2012) PLoS ONE , vol.7
    • Staunstrup, N.H.1    Madsen, J.2    Primo, M.N.3    Li, J.4    Liu, Y.5    Kragh, P.M.6    Li, R.7    Schmidt, M.8    Purup, S.9    Dagnaes-Hansen, F.10
  • 53
    • 79961026115 scopus 로고    scopus 로고
    • Comparative Genomic Integration Profiling of Sleeping Beauty Transposons Mobilized With High Efficacy From Integrase-defective Lentiviral Vectors in Primary Human Cells
    • Moldt, B., Miskey, C, Staunstrup, N.H., Gogol-Doring, A., Bak, R.O., Sharma, N., Mates, L., Izsvak, Z., Chen, W., Ivies, Z. et al. (2011) Comparative Genomic Integration Profiling of Sleeping Beauty Transposons Mobilized With High Efficacy From Integrase-defective Lentiviral Vectors in Primary Human Cells. Mol. Then, 19, 1499-1510.
    • (2011) Mol. Then , vol.19 , pp. 1499-1510
    • Moldt, B.1    Miskey, C.2    Staunstrup, N.H.3    Gogol-Doring, A.4    Bak, R.O.5    Sharma, N.6    Mates, L.7    Izsvak, Z.8    Chen, W.9    Ivies, Z.10
  • 56
    • 84872556705 scopus 로고    scopus 로고
    • Potent microRNA suppression by RNA Pol II-transcribed Tough Decoy inhibitors
    • Bak, R.O., Hollensen, A.K., Primo, M.N., Sorensen, CD. and Mikkelsen, J.G. (2013) Potent microRNA suppression by RNA Pol II-transcribed Tough Decoy inhibitors. RNA, 19, 280-293.
    • (2013) RNA , vol.19 , pp. 280-293
    • Bak, R.O.1    Hollensen, A.K.2    Primo, M.N.3    Sorensen, C.D.4    Mikkelsen, J.G.5


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