AAV-mediated gene therapy for retinal disorders: From mouse to man

Gene Therapy

Volumn 15, Issue 11, 2008, Pages 849-857

  Buch, P K ^a   Bainbridge, J W ^a   Ali, R R ^a  

^a UNIVERSITY COLLEGE LONDON   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; ANGIOSTATIN; BASIC FIBROBLAST GROWTH FACTOR; BRAIN DERIVED NEUROTROPHIC FACTOR; CATALASE; CHANNEL RHODOPSIN 2; CILIARY NEUROTROPHIC FACTOR; ENDOSTATIN; GENE THERAPY AGENT; GLIAL CELL LINE DERIVED NEUROTROPHIC FACTOR; GUANOSINE TRIPHOSPHATASE REGULATOR INTERACTING PROTEIN; INTERLEUKIN 10; MANGANESE SUPEROXIDE DISMUTASE; OCULAR ALBINISM 1 PROTEIN; PARVOVIRUS VECTOR; PERIPHERIN; PIGMENT EPITHELIUM DERIVED FACTOR; PROTEIN BCL XL; PROTEIN MERTK; RETINA PIGMENT EPITHELIUM 65 PROTEIN; RETINOSCHISIN; RHODOPSIN KINASE; SHORT HAIRPIN RNA; VASCULOTROPIN RECEPTOR 1; ZINC FINGER PROTEIN;

ALLERGIC ENCEPHALOMYELITIS; CLINICAL TRIAL; DOSE RESPONSE; DRUG EFFICACY; DRUG MECHANISM; DRUG POTENCY; DRUG POTENTIATION; DRUG SAFETY; DRUG TOLERABILITY; GENE EXPRESSION; GENE REPLACEMENT THERAPY; GENETIC TRANSDUCTION; HUMAN; IMMUNOGENICITY; LEBER CONGENITAL AMAUROSIS; LOW DRUG DOSE; NEUROPROTECTION; NONHUMAN; OCULAR ALBINISM; OPTIC NERVE DISEASE; PRIORITY JOURNAL; RETINA DISEASE; RETINA DYSTROPHY; RETINA MACULA AGE RELATED DEGENERATION; RETINA PIGMENT DEGENERATION; RETINITIS PIGMENTOSA; RETINOSCHISIS; REVIEW; RNA INTERFERENCE; TRANSGENE; UVEITIS; VIRAL GENE DELIVERY SYSTEM; VIRAL GENE THERAPY; VIRUS RECOMBINANT;

ANIMALS; DEPENDOVIRUS; GENE THERAPY; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; HUMANS; MICE; MODELS, ANIMAL; RETINAL DISEASES; SAFETY;

ADENO-ASSOCIATED VIRUS; ANIMALIA;

EID: 44049100684     PISSN: 09697128     EISSN: 14765462     Source Type: Journal    
DOI: 10.1038/gt.2008.66     Document Type: Review

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