Phenotype correction of Fanconi anemia group A hematopoietic stem cells using lentiviral vector

Molecular Therapy

Volumn 8, Issue 4, 2003, Pages 600-610

  Yamada, Kaoru ^a   Ramezani, Ali ^b   Hawley, Robert G ^b   Ebell, Wolfram ^c   Arwert, Fre ^d   Arnold, Larry W ^e   Walsh, Christopher E ^a  

^a MOUNT SINAI SCHOOL OF MEDICINE   (United States)

^b HOLLAND LABORATORY   (United States)

^c CHARITÉ UNIVERSITÄTSMEDIZIN BERLIN   (Germany)

^d VU UNIVERSITY MEDICAL CENTER   (Netherlands)

^e UNIVERSITY OF NORTH CAROLINA   (United States)

Author keywords

Bone marrow reconstitution; Fanca knockout mice; Lentiviral gene transfer; SP cell

Indexed keywords

COMPLEMENTARY DNA; LENTIVIRUS VECTOR; MITOMYCIN C;

ANIMAL EXPERIMENT; BONE MARROW CELL; CELL DEATH; CELL ISOLATION; CELL POPULATION; CELL SELECTION; CHROMOSOME ABERRATION; CONTROLLED STUDY; DNA CROSS LINKING; FANCONI ANEMIA; GENE THERAPY; GENE TRANSFER; GENETIC TRANSFECTION; HEMATOPOIESIS; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HUMAN IMMUNODEFICIENCY VIRUS 1; IN VIVO STUDY; KNOCKOUT MOUSE; MOLONEY LEUKEMIA ONCOVIRUS; MOUSE; NONHUMAN; PHENOTYPE; POLYMERASE CHAIN REACTION; REVIEW; VIRUS GENOME;

ANIMALIA; HUMAN IMMUNODEFICIENCY VIRUS; HUMAN IMMUNODEFICIENCY VIRUS 1; LENTIVIRUS; MOLONEY MURINE LEUKEMIA VIRUS; MURINAE; MURINE LEUKEMIA VIRUS; MURINE STEM CELL RETROVIRAL VECTOR; ONCOVIRINAE;

EID: 0142150968     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1016/S1525-0016(03)00223-5     Document Type: Article

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